Real‐Life Effectiveness After Switching to Avalglucosidase Alfa in Late‐Onset Pompe Disease Patients Worsening on Alglucosidase Alfa Therapy: A French Cohort Study.

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Title: Real‐Life Effectiveness After Switching to Avalglucosidase Alfa in Late‐Onset Pompe Disease Patients Worsening on Alglucosidase Alfa Therapy: A French Cohort Study.
Authors: Tard, Céline1,2 (AUTHOR) celine.tard@chru‐lille.fr, Sacconi, Sabrina3 (AUTHOR), Taouagh, Nadjib2,4 (AUTHOR), Bouhour, Françoise5,6 (AUTHOR), Michaud, Maud2,7 (AUTHOR), Beltran, Stephane8 (AUTHOR), Fournier, Maxime2,9 (AUTHOR), Demurger, Florence10 (AUTHOR), Lagrange, Emmeline11 (AUTHOR), Nollet, Sylvain2,12 (AUTHOR), Noury, Jean‐Baptiste13,14 (AUTHOR), Magot, Armelle13,15 (AUTHOR), Cintas, Pascal16 (AUTHOR), Renard, Dimitri13,17 (AUTHOR), Deibener‐Kaminsky, Joëlle18 (AUTHOR), Lefeuvre, Claire2,4 (AUTHOR), Davion, Jean‐Baptiste1,2 (AUTHOR), Salort‐Campana, Emmanuelle6,19 (AUTHOR), Arrassi, Azzeddine20 (AUTHOR), Spinazzi, Marco21 (AUTHOR)
Source: European Journal of Neurology. Jul2026, Vol. 33 Issue 7, p1-8. 8p.
Database: Academic Search Ultimate
Description
ISSN:13515101
DOI:10.1111/ene.70680