Real‐Life Effectiveness After Switching to Avalglucosidase Alfa in Late‐Onset Pompe Disease Patients Worsening on Alglucosidase Alfa Therapy: A French Cohort Study.
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| Title: | Real‐Life Effectiveness After Switching to Avalglucosidase Alfa in Late‐Onset Pompe Disease Patients Worsening on Alglucosidase Alfa Therapy: A French Cohort Study. |
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| Authors: | Tard, Céline1,2 (AUTHOR) celine.tard@chru‐lille.fr, Sacconi, Sabrina3 (AUTHOR), Taouagh, Nadjib2,4 (AUTHOR), Bouhour, Françoise5,6 (AUTHOR), Michaud, Maud2,7 (AUTHOR), Beltran, Stephane8 (AUTHOR), Fournier, Maxime2,9 (AUTHOR), Demurger, Florence10 (AUTHOR), Lagrange, Emmeline11 (AUTHOR), Nollet, Sylvain2,12 (AUTHOR), Noury, Jean‐Baptiste13,14 (AUTHOR), Magot, Armelle13,15 (AUTHOR), Cintas, Pascal16 (AUTHOR), Renard, Dimitri13,17 (AUTHOR), Deibener‐Kaminsky, Joëlle18 (AUTHOR), Lefeuvre, Claire2,4 (AUTHOR), Davion, Jean‐Baptiste1,2 (AUTHOR), Salort‐Campana, Emmanuelle6,19 (AUTHOR), Arrassi, Azzeddine20 (AUTHOR), Spinazzi, Marco21 (AUTHOR) |
| Source: | European Journal of Neurology. Jul2026, Vol. 33 Issue 7, p1-8. 8p. |
| Database: | Academic Search Ultimate |
| FullText | Text: Availability: 0 |
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| Header | DbId: asn DbLabel: Academic Search Ultimate An: 195682201 AccessLevel: 2 PubType: Academic Journal PubTypeId: academicJournal PreciseRelevancyScore: 0 |
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| Items | – Name: Title Label: Title Group: Ti Data: Real‐Life Effectiveness After Switching to Avalglucosidase Alfa in Late‐Onset Pompe Disease Patients Worsening on Alglucosidase Alfa Therapy: A French Cohort Study. – Name: Author Label: Authors Group: Au Data: <searchLink fieldCode="AR" term="%22Tard%2C+Céline%22">Tard, Céline</searchLink><relatesTo>1,2</relatesTo> (AUTHOR)<i> celine.tard@chru‐lille.fr</i><br /><searchLink fieldCode="AR" term="%22Sacconi%2C+Sabrina%22">Sacconi, Sabrina</searchLink><relatesTo>3</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Taouagh%2C+Nadjib%22">Taouagh, Nadjib</searchLink><relatesTo>2,4</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Bouhour%2C+Françoise%22">Bouhour, Françoise</searchLink><relatesTo>5,6</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Michaud%2C+Maud%22">Michaud, Maud</searchLink><relatesTo>2,7</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Beltran%2C+Stephane%22">Beltran, Stephane</searchLink><relatesTo>8</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Fournier%2C+Maxime%22">Fournier, Maxime</searchLink><relatesTo>2,9</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Demurger%2C+Florence%22">Demurger, Florence</searchLink><relatesTo>10</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Lagrange%2C+Emmeline%22">Lagrange, Emmeline</searchLink><relatesTo>11</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Nollet%2C+Sylvain%22">Nollet, Sylvain</searchLink><relatesTo>2,12</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Noury%2C+Jean‐Baptiste%22">Noury, Jean‐Baptiste</searchLink><relatesTo>13,14</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Magot%2C+Armelle%22">Magot, Armelle</searchLink><relatesTo>13,15</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Cintas%2C+Pascal%22">Cintas, Pascal</searchLink><relatesTo>16</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Renard%2C+Dimitri%22">Renard, Dimitri</searchLink><relatesTo>13,17</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Deibener‐Kaminsky%2C+Joëlle%22">Deibener‐Kaminsky, Joëlle</searchLink><relatesTo>18</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Lefeuvre%2C+Claire%22">Lefeuvre, Claire</searchLink><relatesTo>2,4</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Davion%2C+Jean‐Baptiste%22">Davion, Jean‐Baptiste</searchLink><relatesTo>1,2</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Salort‐Campana%2C+Emmanuelle%22">Salort‐Campana, Emmanuelle</searchLink><relatesTo>6,19</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Arrassi%2C+Azzeddine%22">Arrassi, Azzeddine</searchLink><relatesTo>20</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Spinazzi%2C+Marco%22">Spinazzi, Marco</searchLink><relatesTo>21</relatesTo> (AUTHOR) – Name: TitleSource Label: Source Group: Src Data: <searchLink fieldCode="JN" term="%22European+Journal+of+Neurology%22">European Journal of Neurology</searchLink>. Jul2026, Vol. 33 Issue 7, p1-8. 8p. |
| PLink | https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=asn&AN=195682201 |
| RecordInfo | BibRecord: BibEntity: Identifiers: – Type: doi Value: 10.1111/ene.70680 Languages: – Code: eng Text: English PhysicalDescription: Pagination: PageCount: 8 StartPage: 1 Titles: – TitleFull: Real‐Life Effectiveness After Switching to Avalglucosidase Alfa in Late‐Onset Pompe Disease Patients Worsening on Alglucosidase Alfa Therapy: A French Cohort Study. Type: main BibRelationships: HasContributorRelationships: – PersonEntity: Name: NameFull: Tard, Céline – PersonEntity: Name: NameFull: Sacconi, Sabrina – PersonEntity: Name: NameFull: Taouagh, Nadjib – PersonEntity: Name: NameFull: Bouhour, Françoise – PersonEntity: Name: NameFull: Michaud, Maud – PersonEntity: Name: NameFull: Beltran, Stephane – PersonEntity: Name: NameFull: Fournier, Maxime – PersonEntity: Name: NameFull: Demurger, Florence – PersonEntity: Name: NameFull: Lagrange, Emmeline – PersonEntity: Name: NameFull: Nollet, Sylvain – PersonEntity: Name: NameFull: Noury, Jean‐Baptiste – PersonEntity: Name: NameFull: Magot, Armelle – PersonEntity: Name: NameFull: Cintas, Pascal – PersonEntity: Name: NameFull: Renard, Dimitri – PersonEntity: Name: NameFull: Deibener‐Kaminsky, Joëlle – PersonEntity: Name: NameFull: Lefeuvre, Claire – PersonEntity: Name: NameFull: Davion, Jean‐Baptiste – PersonEntity: Name: NameFull: Salort‐Campana, Emmanuelle – PersonEntity: Name: NameFull: Arrassi, Azzeddine – PersonEntity: Name: NameFull: Spinazzi, Marco IsPartOfRelationships: – BibEntity: Dates: – D: 01 M: 07 Text: Jul2026 Type: published Y: 2026 Identifiers: – Type: issn-print Value: 13515101 Numbering: – Type: volume Value: 33 – Type: issue Value: 7 Titles: – TitleFull: European Journal of Neurology Type: main |
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