Real‐Life Effectiveness After Switching to Avalglucosidase Alfa in Late‐Onset Pompe Disease Patients Worsening on Alglucosidase Alfa Therapy: A French Cohort Study.

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Title: Real‐Life Effectiveness After Switching to Avalglucosidase Alfa in Late‐Onset Pompe Disease Patients Worsening on Alglucosidase Alfa Therapy: A French Cohort Study.
Authors: Tard, Céline1,2 (AUTHOR) celine.tard@chru‐lille.fr, Sacconi, Sabrina3 (AUTHOR), Taouagh, Nadjib2,4 (AUTHOR), Bouhour, Françoise5,6 (AUTHOR), Michaud, Maud2,7 (AUTHOR), Beltran, Stephane8 (AUTHOR), Fournier, Maxime2,9 (AUTHOR), Demurger, Florence10 (AUTHOR), Lagrange, Emmeline11 (AUTHOR), Nollet, Sylvain2,12 (AUTHOR), Noury, Jean‐Baptiste13,14 (AUTHOR), Magot, Armelle13,15 (AUTHOR), Cintas, Pascal16 (AUTHOR), Renard, Dimitri13,17 (AUTHOR), Deibener‐Kaminsky, Joëlle18 (AUTHOR), Lefeuvre, Claire2,4 (AUTHOR), Davion, Jean‐Baptiste1,2 (AUTHOR), Salort‐Campana, Emmanuelle6,19 (AUTHOR), Arrassi, Azzeddine20 (AUTHOR), Spinazzi, Marco21 (AUTHOR)
Source: European Journal of Neurology. Jul2026, Vol. 33 Issue 7, p1-8. 8p.
Database: Academic Search Ultimate
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  Data: Real‐Life Effectiveness After Switching to Avalglucosidase Alfa in Late‐Onset Pompe Disease Patients Worsening on Alglucosidase Alfa Therapy: A French Cohort Study.
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  Data: <searchLink fieldCode="JN" term="%22European+Journal+of+Neurology%22">European Journal of Neurology</searchLink>. Jul2026, Vol. 33 Issue 7, p1-8. 8p.
PLink https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=asn&AN=195682201
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        Value: 10.1111/ene.70680
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        Text: English
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      – TitleFull: Real‐Life Effectiveness After Switching to Avalglucosidase Alfa in Late‐Onset Pompe Disease Patients Worsening on Alglucosidase Alfa Therapy: A French Cohort Study.
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              Text: Jul2026
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              Y: 2026
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