Hyperactive Sleeping Beauty Transposase Enables Persistent Phenotypic Correction in Mice and a Canine Model for Hemophilia B.
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| Title: | Hyperactive Sleeping Beauty Transposase Enables Persistent Phenotypic Correction in Mice and a Canine Model for Hemophilia B. |
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| Authors: | Hausl, Martin A.1, Wenli Zhang1, Müther, Nadine1, Rauschhuber, Christina1, Franck, Helen G.2, Merricks, Elizabeth P.2, Nichols, Timothy C.2, Kay, Mark A.3,4, Ehrhardt, Anja1 ehrhardt@mvp.uni-muenchen.de |
| Source: | Molecular Therapy. Nov2010, Vol. 18 Issue 11, p1896-1906. 11p. |
| Database: | Academic Search Ultimate |
| ISSN: | 15250016 |
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| DOI: | 10.1038/mt.2010.169 |