Efficacy and Safety of Long-term Prophylaxis in Severe Hemophilia A Dogs Following Liver Gene Therapy Using AAV Vectors.

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Bibliographic Details
Title: Efficacy and Safety of Long-term Prophylaxis in Severe Hemophilia A Dogs Following Liver Gene Therapy Using AAV Vectors.
Authors: Sabatino, Denise E.1 dsabatin@mail.med.upenn.edu, Lange, Amy M.1, Altynova, Ekaterina S.1, Sarkar, Rita1, Shangzhen Zhou2, Merricks, Elizabeth P.3, Franck, Helen G.3, Nichols, Timothy C.3, Arruda, Valder R.1,4, Kazazian Jr, Haig H.1
Source: Molecular Therapy. Mar2011, Vol. 19 Issue 3, p442-449. 8p.
Database: Academic Search Ultimate
Description
ISSN:15250016
DOI:10.1038/mt.2010.240