Efficacy and Safety of Long-term Prophylaxis in Severe Hemophilia A Dogs Following Liver Gene Therapy Using AAV Vectors.
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| Title: | Efficacy and Safety of Long-term Prophylaxis in Severe Hemophilia A Dogs Following Liver Gene Therapy Using AAV Vectors. |
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| Authors: | Sabatino, Denise E.1 dsabatin@mail.med.upenn.edu, Lange, Amy M.1, Altynova, Ekaterina S.1, Sarkar, Rita1, Shangzhen Zhou2, Merricks, Elizabeth P.3, Franck, Helen G.3, Nichols, Timothy C.3, Arruda, Valder R.1,4, Kazazian Jr, Haig H.1 |
| Source: | Molecular Therapy. Mar2011, Vol. 19 Issue 3, p442-449. 8p. |
| Database: | Academic Search Ultimate |
| ISSN: | 15250016 |
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| DOI: | 10.1038/mt.2010.240 |