Efficacy and Safety of Long-term Prophylaxis in Severe Hemophilia A Dogs Following Liver Gene Therapy Using AAV Vectors.
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| Title: | Efficacy and Safety of Long-term Prophylaxis in Severe Hemophilia A Dogs Following Liver Gene Therapy Using AAV Vectors. |
|---|---|
| Authors: | Sabatino, Denise E.1 dsabatin@mail.med.upenn.edu, Lange, Amy M.1, Altynova, Ekaterina S.1, Sarkar, Rita1, Shangzhen Zhou2, Merricks, Elizabeth P.3, Franck, Helen G.3, Nichols, Timothy C.3, Arruda, Valder R.1,4, Kazazian Jr, Haig H.1 |
| Source: | Molecular Therapy. Mar2011, Vol. 19 Issue 3, p442-449. 8p. |
| Database: | Academic Search Ultimate |
| FullText | Links: – Type: pdflink Text: Availability: 0 |
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| Header | DbId: asn DbLabel: Academic Search Ultimate An: 58701273 AccessLevel: 2 PubType: Academic Journal PubTypeId: academicJournal PreciseRelevancyScore: 0 |
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| PLink | https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=asn&AN=58701273 |
| RecordInfo | BibRecord: BibEntity: Identifiers: – Type: doi Value: 10.1038/mt.2010.240 Languages: – Code: eng Text: English PhysicalDescription: Pagination: PageCount: 8 StartPage: 442 Titles: – TitleFull: Efficacy and Safety of Long-term Prophylaxis in Severe Hemophilia A Dogs Following Liver Gene Therapy Using AAV Vectors. Type: main BibRelationships: HasContributorRelationships: – PersonEntity: Name: NameFull: Sabatino, Denise E. – PersonEntity: Name: NameFull: Lange, Amy M. – PersonEntity: Name: NameFull: Altynova, Ekaterina S. – PersonEntity: Name: NameFull: Sarkar, Rita – PersonEntity: Name: NameFull: Shangzhen Zhou – PersonEntity: Name: NameFull: Merricks, Elizabeth P. – PersonEntity: Name: NameFull: Franck, Helen G. – PersonEntity: Name: NameFull: Nichols, Timothy C. – PersonEntity: Name: NameFull: Arruda, Valder R. – PersonEntity: Name: NameFull: Kazazian Jr, Haig H. IsPartOfRelationships: – BibEntity: Dates: – D: 01 M: 03 Text: Mar2011 Type: published Y: 2011 Identifiers: – Type: issn-print Value: 15250016 Numbering: – Type: volume Value: 19 – Type: issue Value: 3 Titles: – TitleFull: Molecular Therapy Type: main |
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