Phase 1 dose-escalation study of a siRNA targeting the RTP801 gene in age-related macular degeneration patients.
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| Title: | Phase 1 dose-escalation study of a siRNA targeting the RTP801 gene in age-related macular degeneration patients. |
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| Authors: | Nguyen, Q D1, Schachar, R A2, Nduaka, C I2, Sperling, M2, Basile, A S2, Klamerus, K J2, Chi-Burris, K2, Yan, E2, Paggiarino, D A2, Rosenblatt, I3, Khan, A4, Aitchison, R4, Erlich, S S4 |
| Source: | Eye (0950-222X). Aug2012, Vol. 26 Issue 8, p1099-1105. 7p. |
| Database: | Academic Search Ultimate |
| ISSN: | 0950222X |
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| DOI: | 10.1038/eye.2012.106 |