Fabry disease in children: agalsidase-beta enzyme replacement therapy.
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| Title: | Fabry disease in children: agalsidase-beta enzyme replacement therapy. |
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| Authors: | Borgwardt, L1, Feldt‐Rasmussen, U2, Rasmussen, AK2, Ballegaard, M3, Meldgaard Lund, A1 |
| Source: | Clinical Genetics. May2013, Vol. 83 Issue 5, p432-438. 7p. 2 Charts, 3 Graphs. |
| Database: | Academic Search Ultimate |
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| ISSN: | 00099163 |
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| DOI: | 10.1111/j.1399-0004.2012.01947.x |