Systemic delivery of triplex-forming PNA and donor DNA by nanoparticles mediates site-specific genome editing of human hematopoietic cells in vivo.
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| Title: | Systemic delivery of triplex-forming PNA and donor DNA by nanoparticles mediates site-specific genome editing of human hematopoietic cells in vivo. |
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| Authors: | McNeer, N A1, Schleifman, E B2, Cuthbert, A3, Brehm, M3, Jackson, A4, Cheng, C1, Anandalingam, K1, Kumar, P4, Shultz, L D5, Greiner, D L3, Mark Saltzman, W1, Glazer, P M6 |
| Source: | Gene Therapy. Jun2013, Vol. 20 Issue 6, p658-669. 12p. 4 Diagrams, 3 Charts, 5 Graphs. |
| Database: | Academic Search Ultimate |
| ISSN: | 09697128 |
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| DOI: | 10.1038/gt.2012.82 |
