P.4.10 Exon skipping as a therapeutic strategy applied to a RyR1 mutation causing severe core myopathy.
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| Title: | P.4.10 Exon skipping as a therapeutic strategy applied to a RyR1 mutation causing severe core myopathy. |
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| Authors: | Brocard, J.1, Monnier, N.2, Piétri-Rouxel, F.3, Garcia, L.3, Lunardi, J.1, Fauré, J.1, Fourest-Lieuvin, A.1, Marty, I.1 |
| Source: | Neuromuscular Disorders. Oct2013, Vol. 23 Issue 9/10, p762-762. 1p. |
| Database: | Academic Search Ultimate |
| ISSN: | 09608966 |
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| DOI: | 10.1016/j.nmd.2013.06.448 |