P.4.10 Exon skipping as a therapeutic strategy applied to a RyR1 mutation causing severe core myopathy.

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Bibliographic Details
Title: P.4.10 Exon skipping as a therapeutic strategy applied to a RyR1 mutation causing severe core myopathy.
Authors: Brocard, J.1, Monnier, N.2, Piétri-Rouxel, F.3, Garcia, L.3, Lunardi, J.1, Fauré, J.1, Fourest-Lieuvin, A.1, Marty, I.1
Source: Neuromuscular Disorders. Oct2013, Vol. 23 Issue 9/10, p762-762. 1p.
Database: Academic Search Ultimate
Description
ISSN:09608966
DOI:10.1016/j.nmd.2013.06.448