CEP290 gene transfer rescues Leber congenital amaurosis cellular phenotype.

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Bibliographic Details
Title: CEP290 gene transfer rescues Leber congenital amaurosis cellular phenotype.
Authors: Burnight, E R1, Wiley, L A1, Drack, A V1, Braun, T A2, Anfinson, K R1, Kaalberg, E E1, Halder, J A1, Affatigato, L M1, Mullins, R F1, Stone, E M3, Tucker, B A1
Source: Gene Therapy. Jul2014, Vol. 21 Issue 7, p662-672. 11p.
Database: Academic Search Ultimate
Description
ISSN:09697128
DOI:10.1038/gt.2014.39