CEP290 gene transfer rescues Leber congenital amaurosis cellular phenotype.
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| Title: | CEP290 gene transfer rescues Leber congenital amaurosis cellular phenotype. |
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| Authors: | Burnight, E R1, Wiley, L A1, Drack, A V1, Braun, T A2, Anfinson, K R1, Kaalberg, E E1, Halder, J A1, Affatigato, L M1, Mullins, R F1, Stone, E M3, Tucker, B A1 |
| Source: | Gene Therapy. Jul2014, Vol. 21 Issue 7, p662-672. 11p. |
| Database: | Academic Search Ultimate |
| ISSN: | 09697128 |
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| DOI: | 10.1038/gt.2014.39 |