Enzyme replacement therapy and extended newborn screening for mucopolysaccharidoses: opinions of treating physicians.

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Bibliographic Details
Title: Enzyme replacement therapy and extended newborn screening for mucopolysaccharidoses: opinions of treating physicians.
Authors: Coman DJ; Bruce Lefroy Centre for Genetic Health Research, Murdoch Childrens Research Institute, 10th Floor, Royal Children's Hospital, Flemington Road, Parkville, 3052, Victoria, Australia., Hayes IM, Collins V, Sahhar M, Wraith JE, Delatycki MB
Source: JIMD reports [JIMD Rep] 2011; Vol. 1, pp. 9-15. Date of Electronic Publication: 2011 Jun 22.
Publication Type: Journal Article
Journal Info: Publisher: Wiley Country of Publication: United States NLM ID: 101568557 Publication Model: Print-Electronic Cited Medium: Print ISSN: 2192-8304 (Print) Linking ISSN: 21928304 NLM ISO Abbreviation: JIMD Rep Subsets: PubMed not MEDLINE
Database: MEDLINE Ultimate
Description
ISSN:2192-8304
DOI:10.1007/8904_2011_9