| Authors: |
Mistry PK; Department of Internal Medicine, Yale University School of Medicine, New Haven, Connecticut., Batista JL; Sanofi Genzyme, Cambridge, Massachusetts., Andersson HC; Hayward Genetics Center, Tulane University Medical School, New Orleans, Louisiana., Balwani M; Icahn School of Medicine at Mount Sinai, New York City, New York., Burrow TA; College of Medicine, University of Arkansas for Medical Sciences, Little Rock, Arkansas., Charrow J; Northwestern University Feinberg School of Medicine, Chicago, Illinois., Kaplan P; Children's Hospital of Philadelphia, Philadelphia, Pennsylvania., Khan A; The University of Calgary, Calgary, Alberta, Canada., Kishnani PS; Division of Medical Genetics, Duke University School of Medicine, Durham, North Carolina., Kolodny EH; New York University School of Medicine, New York, New York., Rosenbloom B; Cedars-Sinai/Tower Hematology Oncology, Beverly Hills, California., Scott CR; University of Washington, Seattle, Washington., Weinreb N; Departments of Human Genetics and Medicine (Hematology), University of Miami Miller School of Medicine, Miami, Florida. |