Genome editing in mitochondria corrects a pathogenic mtDNA mutation in vivo.

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Bibliographic Details
Title: Genome editing in mitochondria corrects a pathogenic mtDNA mutation in vivo.
Authors: Gammage PA; MRC Mitochondrial Biology Unit, University of Cambridge, Cambridge, UK. payam.gammage@mrc-mbu.cam.ac.uk., Viscomi C; MRC Mitochondrial Biology Unit, University of Cambridge, Cambridge, UK., Simard ML; Max Planck Institute for Biology of Ageing, Cologne, Germany., Costa ASH; MRC Cancer Unit, University of Cambridge, Cambridge, UK., Gaude E; MRC Cancer Unit, University of Cambridge, Cambridge, UK., Powell CA; MRC Mitochondrial Biology Unit, University of Cambridge, Cambridge, UK., Van Haute L; MRC Mitochondrial Biology Unit, University of Cambridge, Cambridge, UK., McCann BJ; MRC Mitochondrial Biology Unit, University of Cambridge, Cambridge, UK., Rebelo-Guiomar P; MRC Mitochondrial Biology Unit, University of Cambridge, Cambridge, UK.; Graduate Program in Areas of Basic and Applied Biology (GABBA), University of Porto, Porto, Portugal., Cerutti R; MRC Mitochondrial Biology Unit, University of Cambridge, Cambridge, UK., Zhang L; Sangamo Therapeutics Inc., Richmond, CA, USA., Rebar EJ; Sangamo Therapeutics Inc., Richmond, CA, USA., Zeviani M; MRC Mitochondrial Biology Unit, University of Cambridge, Cambridge, UK., Frezza C; MRC Cancer Unit, University of Cambridge, Cambridge, UK., Stewart JB; Max Planck Institute for Biology of Ageing, Cologne, Germany., Minczuk M; MRC Mitochondrial Biology Unit, University of Cambridge, Cambridge, UK. michal.minczuk@mrc-mbu.cam.ac.uk.
Source: Nature medicine [Nat Med] 2018 Nov; Vol. 24 (11), pp. 1691-1695. Date of Electronic Publication: 2018 Sep 24.
Publication Type: Journal Article; Research Support, Non-U.S. Gov't
Journal Info: Publisher: Nature Publishing Company Country of Publication: United States NLM ID: 9502015 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1546-170X (Electronic) Linking ISSN: 10788956 NLM ISO Abbreviation: Nat Med Subsets: MEDLINE
Database: MEDLINE Ultimate
Description
ISSN:1546-170X
DOI:10.1038/s41591-018-0165-9