Antigen-selective modulation of AAV immunogenicity with tolerogenic rapamycin nanoparticles enables successful vector re-administration.

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Title: Antigen-selective modulation of AAV immunogenicity with tolerogenic rapamycin nanoparticles enables successful vector re-administration.
Authors: Meliani A; Sorbonne Université and INSERM U974, 105 boulevard de l'Hôpital, 75651, Paris, France.; Genethon, UMR_S951 Inserm, Univ Evry, Université Paris Saclay, EPHE, 1 bis rue de l'Internationale, 91000, Evry, France., Boisgerault F; Genethon, UMR_S951 Inserm, Univ Evry, Université Paris Saclay, EPHE, 1 bis rue de l'Internationale, 91000, Evry, France., Hardet R; Sorbonne Université and INSERM U974, 105 boulevard de l'Hôpital, 75651, Paris, France., Marmier S; Sorbonne Université and INSERM U974, 105 boulevard de l'Hôpital, 75651, Paris, France., Collaud F; Genethon, UMR_S951 Inserm, Univ Evry, Université Paris Saclay, EPHE, 1 bis rue de l'Internationale, 91000, Evry, France., Ronzitti G; Genethon, UMR_S951 Inserm, Univ Evry, Université Paris Saclay, EPHE, 1 bis rue de l'Internationale, 91000, Evry, France., Leborgne C; Genethon, UMR_S951 Inserm, Univ Evry, Université Paris Saclay, EPHE, 1 bis rue de l'Internationale, 91000, Evry, France., Costa Verdera H; Sorbonne Université and INSERM U974, 105 boulevard de l'Hôpital, 75651, Paris, France.; Genethon, UMR_S951 Inserm, Univ Evry, Université Paris Saclay, EPHE, 1 bis rue de l'Internationale, 91000, Evry, France., Simon Sola M; Sorbonne Université and INSERM U974, 105 boulevard de l'Hôpital, 75651, Paris, France.; Genethon, UMR_S951 Inserm, Univ Evry, Université Paris Saclay, EPHE, 1 bis rue de l'Internationale, 91000, Evry, France., Charles S; Genethon, UMR_S951 Inserm, Univ Evry, Université Paris Saclay, EPHE, 1 bis rue de l'Internationale, 91000, Evry, France., Vignaud A; Genethon, UMR_S951 Inserm, Univ Evry, Université Paris Saclay, EPHE, 1 bis rue de l'Internationale, 91000, Evry, France., van Wittenberghe L; Genethon, UMR_S951 Inserm, Univ Evry, Université Paris Saclay, EPHE, 1 bis rue de l'Internationale, 91000, Evry, France., Manni G; Department of Experimental Medicine, University of Perugia, Piazzale Gambuli, 1, 06132, Perugia, Italy., Christophe O; INSERM U1176 and Unité Mixte de Recherche S1176, Université Paris-Sud, Kremlin-Bicetre, 63 rue Gabriel Péri, 94270, Paris, France., Fallarino F; Department of Experimental Medicine, University of Perugia, Piazzale Gambuli, 1, 06132, Perugia, Italy., Roy C; Selecta Bioscience, 480 Arsenal Street, Watertown, MA, 02472, USA., Michaud A; Selecta Bioscience, 480 Arsenal Street, Watertown, MA, 02472, USA., Ilyinskii P; Selecta Bioscience, 480 Arsenal Street, Watertown, MA, 02472, USA., Kishimoto TK; Selecta Bioscience, 480 Arsenal Street, Watertown, MA, 02472, USA., Mingozzi F; Sorbonne Université and INSERM U974, 105 boulevard de l'Hôpital, 75651, Paris, France. fmingozzi@genethon.fr.; Genethon, UMR_S951 Inserm, Univ Evry, Université Paris Saclay, EPHE, 1 bis rue de l'Internationale, 91000, Evry, France. fmingozzi@genethon.fr.
Source: Nature communications [Nat Commun] 2018 Oct 05; Vol. 9 (1), pp. 4098. Date of Electronic Publication: 2018 Oct 05.
Publication Type: Journal Article; Research Support, Non-U.S. Gov't
Journal Info: Publisher: Nature Pub. Group Country of Publication: England NLM ID: 101528555 Publication Model: Electronic Cited Medium: Internet ISSN: 2041-1723 (Electronic) Linking ISSN: 20411723 NLM ISO Abbreviation: Nat Commun Subsets: MEDLINE
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  Data: Antigen-selective modulation of AAV immunogenicity with tolerogenic rapamycin nanoparticles enables successful vector re-administration.
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  Data: <searchLink fieldCode="AU" term="%22Meliani+A%22">Meliani A</searchLink>; Sorbonne Université and INSERM U974, 105 boulevard de l'Hôpital, 75651, Paris, France.; Genethon, UMR_S951 Inserm, Univ Evry, Université Paris Saclay, EPHE, 1 bis rue de l'Internationale, 91000, Evry, France.<br /><searchLink fieldCode="AU" term="%22Boisgerault+F%22">Boisgerault F</searchLink>; Genethon, UMR_S951 Inserm, Univ Evry, Université Paris Saclay, EPHE, 1 bis rue de l'Internationale, 91000, Evry, France.<br /><searchLink fieldCode="AU" term="%22Hardet+R%22">Hardet R</searchLink>; Sorbonne Université and INSERM U974, 105 boulevard de l'Hôpital, 75651, Paris, France.<br /><searchLink fieldCode="AU" term="%22Marmier+S%22">Marmier S</searchLink>; Sorbonne Université and INSERM U974, 105 boulevard de l'Hôpital, 75651, Paris, France.<br /><searchLink fieldCode="AU" term="%22Collaud+F%22">Collaud F</searchLink>; Genethon, UMR_S951 Inserm, Univ Evry, Université Paris Saclay, EPHE, 1 bis rue de l'Internationale, 91000, Evry, France.<br /><searchLink fieldCode="AU" term="%22Ronzitti+G%22">Ronzitti G</searchLink>; Genethon, UMR_S951 Inserm, Univ Evry, Université Paris Saclay, EPHE, 1 bis rue de l'Internationale, 91000, Evry, France.<br /><searchLink fieldCode="AU" term="%22Leborgne+C%22">Leborgne C</searchLink>; Genethon, UMR_S951 Inserm, Univ Evry, Université Paris Saclay, EPHE, 1 bis rue de l'Internationale, 91000, Evry, France.<br /><searchLink fieldCode="AU" term="%22Costa+Verdera+H%22">Costa Verdera H</searchLink>; Sorbonne Université and INSERM U974, 105 boulevard de l'Hôpital, 75651, Paris, France.; Genethon, UMR_S951 Inserm, Univ Evry, Université Paris Saclay, EPHE, 1 bis rue de l'Internationale, 91000, Evry, France.<br /><searchLink fieldCode="AU" term="%22Simon+Sola+M%22">Simon Sola M</searchLink>; Sorbonne Université and INSERM U974, 105 boulevard de l'Hôpital, 75651, Paris, France.; Genethon, UMR_S951 Inserm, Univ Evry, Université Paris Saclay, EPHE, 1 bis rue de l'Internationale, 91000, Evry, France.<br /><searchLink fieldCode="AU" term="%22Charles+S%22">Charles S</searchLink>; Genethon, UMR_S951 Inserm, Univ Evry, Université Paris Saclay, EPHE, 1 bis rue de l'Internationale, 91000, Evry, France.<br /><searchLink fieldCode="AU" term="%22Vignaud+A%22">Vignaud A</searchLink>; Genethon, UMR_S951 Inserm, Univ Evry, Université Paris Saclay, EPHE, 1 bis rue de l'Internationale, 91000, Evry, France.<br /><searchLink fieldCode="AU" term="%22van+Wittenberghe+L%22">van Wittenberghe L</searchLink>; Genethon, UMR_S951 Inserm, Univ Evry, Université Paris Saclay, EPHE, 1 bis rue de l'Internationale, 91000, Evry, France.<br /><searchLink fieldCode="AU" term="%22Manni+G%22">Manni G</searchLink>; Department of Experimental Medicine, University of Perugia, Piazzale Gambuli, 1, 06132, Perugia, Italy.<br /><searchLink fieldCode="AU" term="%22Christophe+O%22">Christophe O</searchLink>; INSERM U1176 and Unité Mixte de Recherche S1176, Université Paris-Sud, Kremlin-Bicetre, 63 rue Gabriel Péri, 94270, Paris, France.<br /><searchLink fieldCode="AU" term="%22Fallarino+F%22">Fallarino F</searchLink>; Department of Experimental Medicine, University of Perugia, Piazzale Gambuli, 1, 06132, Perugia, Italy.<br /><searchLink fieldCode="AU" term="%22Roy+C%22">Roy C</searchLink>; Selecta Bioscience, 480 Arsenal Street, Watertown, MA, 02472, USA.<br /><searchLink fieldCode="AU" term="%22Michaud+A%22">Michaud A</searchLink>; Selecta Bioscience, 480 Arsenal Street, Watertown, MA, 02472, USA.<br /><searchLink fieldCode="AU" term="%22Ilyinskii+P%22">Ilyinskii P</searchLink>; Selecta Bioscience, 480 Arsenal Street, Watertown, MA, 02472, USA.<br /><searchLink fieldCode="AU" term="%22Kishimoto+TK%22">Kishimoto TK</searchLink>; Selecta Bioscience, 480 Arsenal Street, Watertown, MA, 02472, USA.<br /><searchLink fieldCode="AU" term="%22Mingozzi+F%22">Mingozzi F</searchLink>; Sorbonne Université and INSERM U974, 105 boulevard de l'Hôpital, 75651, Paris, France. fmingozzi@genethon.fr.; Genethon, UMR_S951 Inserm, Univ Evry, Université Paris Saclay, EPHE, 1 bis rue de l'Internationale, 91000, Evry, France. fmingozzi@genethon.fr.
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