| Authors: |
Cain JT; Pediatrics and Rare Diseases Group, Sanford Research, Sioux Falls, SD 57104, USA., Likhite S; The Research Institute at Nationwide Children's Hospital, Columbus, OH 43205, USA., White KA; Pediatrics and Rare Diseases Group, Sanford Research, Sioux Falls, SD 57104, USA., Timm DJ; Pediatrics and Rare Diseases Group, Sanford Research, Sioux Falls, SD 57104, USA., Davis SS; Pediatrics and Rare Diseases Group, Sanford Research, Sioux Falls, SD 57104, USA., Johnson TB; Pediatrics and Rare Diseases Group, Sanford Research, Sioux Falls, SD 57104, USA., Dennys-Rivers CN; The Research Institute at Nationwide Children's Hospital, Columbus, OH 43205, USA., Rinaldi F; The Research Institute at Nationwide Children's Hospital, Columbus, OH 43205, USA., Motti D; The Research Institute at Nationwide Children's Hospital, Columbus, OH 43205, USA., Corcoran S; The Research Institute at Nationwide Children's Hospital, Columbus, OH 43205, USA., Morales P; The Mannheimer Foundation, Inc., Homestead, FL 33034, USA., Pierson C; The Research Institute at Nationwide Children's Hospital, Columbus, OH 43205, USA., Hughes SM; Department of Biochemistry, School of Biomedical Sciences, Brain Health Research Centre, University of Otago, Dunedin 9016, New Zealand., Lee SY; Division of Biology, Kansas State University, Manhattan, KS 66506, USA., Kaspar BK; AveXis Inc., Bannockburn, IL 60015, USA., Meyer K; The Research Institute at Nationwide Children's Hospital, Columbus, OH 43205, USA., Weimer JM; Pediatrics and Rare Diseases Group, Sanford Research, Sioux Falls, SD 57104, USA; Department of Pediatrics, Sanford School of Medicine, University of South Dakota, Sioux Falls, SD 57069, USA. Electronic address: jill.weimer@sanfordhealth.org. |