| Authors: |
Ramos DM; Department of Neuroscience and., d'Ydewalle C; Department of Neurology, Johns Hopkins University School of Medicine, Baltimore, Maryland, USA., Gabbeta V; PTC Therapeutics, South Plainfield, New Jersey, USA., Dakka A; PTC Therapeutics, South Plainfield, New Jersey, USA., Klein SK; Ionis Pharmaceuticals, Carlsbad, California, USA., Norris DA; Ionis Pharmaceuticals, Carlsbad, California, USA., Matson J; Ionis Pharmaceuticals, Carlsbad, California, USA., Taylor SJ; PharmOptima, Portage, Michigan, USA., Zaworski PG; PharmOptima, Portage, Michigan, USA., Prior TW; Center for Human Genetics, Case Western Reserve University, Cleveland, Ohio, USA., Snyder PJ; Department of Pathology, Ohio State University, Columbus, Ohio, USA., Valdivia D; Department of Neurology, Johns Hopkins University School of Medicine, Baltimore, Maryland, USA., Hatem CL; Department of Neurology, Johns Hopkins University School of Medicine, Baltimore, Maryland, USA., Waters I; The Sidney Kimmel Comprehensive Cancer Center, Department of Oncology, and., Gupte N; Department of Medicine, Johns Hopkins University School of Medicine, Baltimore, Maryland, USA., Swoboda KJ; Center for Genomic Medicine, Department of Neurology, Massachusetts General Hospital, Harvard Medical School, Boston, Massachusetts, USA., Rigo F; Ionis Pharmaceuticals, Carlsbad, California, USA., Bennett CF; Ionis Pharmaceuticals, Carlsbad, California, USA., Naryshkin N; PTC Therapeutics, South Plainfield, New Jersey, USA., Paushkin S; SMA Foundation, New York, New York, USA., Crawford TO; Department of Neurology, Johns Hopkins University School of Medicine, Baltimore, Maryland, USA.; Department of Pediatrics, Johns Hopkins University School of Medicine, Baltimore, Maryland, USA., Sumner CJ; Department of Neuroscience and.; Department of Neurology, Johns Hopkins University School of Medicine, Baltimore, Maryland, USA. |
