| Authors: |
Wongkittichote P; Children's National Rare Disease Institute, Children's National Health System, Washington DC 20010, United States; Department of Pediatrics, Faculty of Medicine Ramathibodi Hospital, Mahidol University, Bangkok 10400, Thailand; Department of Pediatrics, St. Louis Children's Hospital, Washington University School of Medicine, St. Louis, MO, USA., Cunningham G; Children's National Rare Disease Institute, Children's National Health System, Washington DC 20010, United States., Summar ML; Children's National Rare Disease Institute, Children's National Health System, Washington DC 20010, United States., Pumbo E; Children's National Rare Disease Institute, Children's National Health System, Washington DC 20010, United States., Forny P; Division of Metabolism, the Children's Research Center, The Swiss Newborn Screening Laboratory, University Children's Hospital Zurich, 8032 Zurich, Switzerland; The radiz-Rare Disease Initiative Zurich, Clinical Research Priority Program for Rare Diseases, the Center for Integrative Human Physiology, University of Zurich, 8006 Zurich, Switzerland., Baumgartner MR; Division of Metabolism, the Children's Research Center, The Swiss Newborn Screening Laboratory, University Children's Hospital Zurich, 8032 Zurich, Switzerland; The radiz-Rare Disease Initiative Zurich, Clinical Research Priority Program for Rare Diseases, the Center for Integrative Human Physiology, University of Zurich, 8006 Zurich, Switzerland., Chapman KA; Children's National Rare Disease Institute, Children's National Health System, Washington DC 20010, United States. Electronic address: KChapman@childrensnational.org. |