Formulation and Clinical Evaluation of Sodium Benzoate Oral Solution for the Treatment of Urea Cycle Disorders in Pediatric Patients.

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Title: Formulation and Clinical Evaluation of Sodium Benzoate Oral Solution for the Treatment of Urea Cycle Disorders in Pediatric Patients.
Authors: Maines E; Pediatric Unit, Provincial Centre for Rare Diseases, Department of Women's and Children's Health, 'S. Chiara' Hospital, Azienda Provinciale per i Servizi Sanitari, Largo Medaglie d'oro 9, 38122, Trento, Italy. evelina.maines@apss.tn.it., Urru SAM; Hospital Pharmacy Unit, Azienda Provinciale per i Servizi Sanitari, Largo Medaglie d'oro 9, Trento, Italy., Burri E; Hospital Pharmacy Unit, Azienda Provinciale per i Servizi Sanitari, Largo Medaglie d'oro 9, Trento, Italy., Piccoli G; CIBIO - Centre for integrative biology, Università degli Studi di Trento, Via Sommarive 9, Povo, Trento, Italy.; Dulbecco Telethon Institute, Trento, Italy., Pedrolli A; Pediatric Unit, Provincial Centre for Rare Diseases, Department of Women's and Children's Health, 'S. Chiara' Hospital, Azienda Provinciale per i Servizi Sanitari, Largo Medaglie d'oro 9, 38122, Trento, Italy., Pasqualini A; Hospital Pharmacy Unit, Azienda Provinciale per i Servizi Sanitari, Largo Medaglie d'oro 9, Trento, Italy., Burlina AL; Division of Inherited Metabolic Diseases, Reference Centre Expanded Newborn Screening, Department of Women's and Children's Health, University Hospital, via Giustiniani 2, Padua, Italy., Temporin G; Hospital Pharmacy Unit, Azienda Provinciale per i Servizi Sanitari, Largo Medaglie d'oro 9, Trento, Italy.
Source: AAPS PharmSciTech [AAPS PharmSciTech] 2020 Mar 09; Vol. 21 (3), pp. 100. Date of Electronic Publication: 2020 Mar 09.
Publication Type: Case Reports; Journal Article
Journal Info: Publisher: Springer Country of Publication: United States NLM ID: 100960111 Publication Model: Electronic Cited Medium: Internet ISSN: 1530-9932 (Electronic) Linking ISSN: 15309932 NLM ISO Abbreviation: AAPS PharmSciTech Subsets: MEDLINE
Database: MEDLINE Ultimate
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Description
ISSN:1530-9932
DOI:10.1208/s12249-020-01642-y