Orphan drug clinical development.
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| Title: | Orphan drug clinical development. |
|---|---|
| Authors: | Blin O; Service de pharmacologie clinique et pharmacovigilance, Aix Marseille Univ, AP-HM, INSERM, Inst Neurosci Syst, 13005 Marseille, France; Orphandev-FCRIN, INSERM, 13005 Marseille, France. Electronic address: olivier.blin@ap-hm.fr., Lefebvre MN; Service de pharmacologie clinique et pharmacovigilance, Aix Marseille Univ, AP-HM, INSERM, Inst Neurosci Syst, 13005 Marseille, France; Orphandev-FCRIN, INSERM, 13005 Marseille, France., Rascol O; Services de pharmacologie clinique et neurosciences, centre d'investigation clinique CIC 1436, NS-Park/FCRIN network, NeuroToul COEN center, université de Toulouse UPS, CHU de Toulouse, INSERM, 31000 Toulouse, France., Micallef J; Service de pharmacologie clinique et pharmacovigilance, Aix Marseille Univ, AP-HM, INSERM, Inst Neurosci Syst, 13005 Marseille, France. |
| Source: | Therapie [Therapie] 2020 Apr; Vol. 75 (2), pp. 141-147. Date of Electronic Publication: 2020 Feb 13. |
| Publication Type: | Journal Article; Review |
| Journal Info: | Publisher: Elsevier Masson Country of Publication: France NLM ID: 0420544 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1958-5578 (Electronic) Linking ISSN: 00405957 NLM ISO Abbreviation: Therapie Subsets: MEDLINE |
| Database: | MEDLINE Ultimate |
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