| Authors: |
Pei X; Institute of Hematology and Blood Diseases Hospital, Chinese Academy of Medical Sciences & Peking Union Medical College, Tianjin 300020, China.; Gene Therapy Center, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA., Shao W; Gene Therapy Center, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA., Xing A; Gene Therapy Center, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA., Askew C; Gene Therapy Center, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA., Chen X; Gene Therapy Center, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA., Cui C; Department of Surgery, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA., Abajas YL; Department of Pediatrics, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA., Gerber DA; Department of Surgery, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA., Merricks EP; Department of Pathology and Laboratory Medicine, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA., Nichols TC; Department of Pathology and Laboratory Medicine, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA., Li W; Institute of Pathogen Biology, Chinese Academy of Medical Sciences & Peking Union Medical College, Beijing 100730, China., Samulski RJ; Gene Therapy Center, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA.; Department of Pharmacology, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA., Li C; Gene Therapy Center, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA.; Department of Pediatrics, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA.; Carolina Institute for Developmental Disabilities, University of North Carolina at Chapel Hill, NC 27599, USA. |