Development of AAV Variants with Human Hepatocyte Tropism and Neutralizing Antibody Escape Capacity.

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Title: Development of AAV Variants with Human Hepatocyte Tropism and Neutralizing Antibody Escape Capacity.
Authors: Pei X; Institute of Hematology and Blood Diseases Hospital, Chinese Academy of Medical Sciences & Peking Union Medical College, Tianjin 300020, China.; Gene Therapy Center, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA., Shao W; Gene Therapy Center, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA., Xing A; Gene Therapy Center, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA., Askew C; Gene Therapy Center, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA., Chen X; Gene Therapy Center, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA., Cui C; Department of Surgery, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA., Abajas YL; Department of Pediatrics, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA., Gerber DA; Department of Surgery, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA., Merricks EP; Department of Pathology and Laboratory Medicine, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA., Nichols TC; Department of Pathology and Laboratory Medicine, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA., Li W; Institute of Pathogen Biology, Chinese Academy of Medical Sciences & Peking Union Medical College, Beijing 100730, China., Samulski RJ; Gene Therapy Center, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA.; Department of Pharmacology, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA., Li C; Gene Therapy Center, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA.; Department of Pediatrics, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA.; Carolina Institute for Developmental Disabilities, University of North Carolina at Chapel Hill, NC 27599, USA.
Source: Molecular therapy. Methods & clinical development [Mol Ther Methods Clin Dev] 2020 Jun 03; Vol. 18, pp. 259-268. Date of Electronic Publication: 2020 Jun 03 (Print Publication: 2020).
Publication Type: Journal Article
Journal Info: Publisher: Cell Press Country of Publication: United States NLM ID: 101624857 Publication Model: eCollection Cited Medium: Print ISSN: 2329-0501 (Print) Linking ISSN: 23290501 NLM ISO Abbreviation: Mol Ther Methods Clin Dev Subsets: PubMed not MEDLINE
Database: MEDLINE Ultimate
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  Data: <searchLink fieldCode="AU" term="%22Pei+X%22">Pei X</searchLink>; Institute of Hematology and Blood Diseases Hospital, Chinese Academy of Medical Sciences & Peking Union Medical College, Tianjin 300020, China.; Gene Therapy Center, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA.<br /><searchLink fieldCode="AU" term="%22Shao+W%22">Shao W</searchLink>; Gene Therapy Center, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA.<br /><searchLink fieldCode="AU" term="%22Xing+A%22">Xing A</searchLink>; Gene Therapy Center, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA.<br /><searchLink fieldCode="AU" term="%22Askew+C%22">Askew C</searchLink>; Gene Therapy Center, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA.<br /><searchLink fieldCode="AU" term="%22Chen+X%22">Chen X</searchLink>; Gene Therapy Center, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA.<br /><searchLink fieldCode="AU" term="%22Cui+C%22">Cui C</searchLink>; Department of Surgery, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA.<br /><searchLink fieldCode="AU" term="%22Abajas+YL%22">Abajas YL</searchLink>; Department of Pediatrics, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA.<br /><searchLink fieldCode="AU" term="%22Gerber+DA%22">Gerber DA</searchLink>; Department of Surgery, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA.<br /><searchLink fieldCode="AU" term="%22Merricks+EP%22">Merricks EP</searchLink>; Department of Pathology and Laboratory Medicine, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA.<br /><searchLink fieldCode="AU" term="%22Nichols+TC%22">Nichols TC</searchLink>; Department of Pathology and Laboratory Medicine, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA.<br /><searchLink fieldCode="AU" term="%22Li+W%22">Li W</searchLink>; Institute of Pathogen Biology, Chinese Academy of Medical Sciences & Peking Union Medical College, Beijing 100730, China.<br /><searchLink fieldCode="AU" term="%22Samulski+RJ%22">Samulski RJ</searchLink>; Gene Therapy Center, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA.; Department of Pharmacology, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA.<br /><searchLink fieldCode="AU" term="%22Li+C%22">Li C</searchLink>; Gene Therapy Center, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA.; Department of Pediatrics, University of North Carolina at Chapel Hill, Chapel Hill, NC 27599, USA.; Carolina Institute for Developmental Disabilities, University of North Carolina at Chapel Hill, NC 27599, USA.
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