Investigating the pharmacodynamic durability of GalNAc-siRNA conjugates.
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| Title: | Investigating the pharmacodynamic durability of GalNAc-siRNA conjugates. |
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| Authors: | Brown CR; Alnylam Pharmaceuticals, Inc., Cambridge, MA 02142, USA., Gupta S; Alnylam Pharmaceuticals, Inc., Cambridge, MA 02142, USA., Qin J; Alnylam Pharmaceuticals, Inc., Cambridge, MA 02142, USA., Racie T; Alnylam Pharmaceuticals, Inc., Cambridge, MA 02142, USA., He G; Alnylam Pharmaceuticals, Inc., Cambridge, MA 02142, USA., Lentini S; Alnylam Pharmaceuticals, Inc., Cambridge, MA 02142, USA., Malone R; Alnylam Pharmaceuticals, Inc., Cambridge, MA 02142, USA., Yu M; Alnylam Pharmaceuticals, Inc., Cambridge, MA 02142, USA., Matsuda S; Alnylam Pharmaceuticals, Inc., Cambridge, MA 02142, USA., Shulga-Morskaya S; Alnylam Pharmaceuticals, Inc., Cambridge, MA 02142, USA., Nair AV; MGH Program in Membrane Biology, Division of Nephrology, Massachusetts General Hospital and Harvard Medical School, Boston, MA 02114, USA., Theile CS; Alnylam Pharmaceuticals, Inc., Cambridge, MA 02142, USA., Schmidt K; Alnylam Pharmaceuticals, Inc., Cambridge, MA 02142, USA., Shahraz A; Alnylam Pharmaceuticals, Inc., Cambridge, MA 02142, USA., Goel V; Alnylam Pharmaceuticals, Inc., Cambridge, MA 02142, USA., Parmar RG; Alnylam Pharmaceuticals, Inc., Cambridge, MA 02142, USA., Zlatev I; Alnylam Pharmaceuticals, Inc., Cambridge, MA 02142, USA., Schlegel MK; Alnylam Pharmaceuticals, Inc., Cambridge, MA 02142, USA., Nair JK; Alnylam Pharmaceuticals, Inc., Cambridge, MA 02142, USA., Jayaraman M; Alnylam Pharmaceuticals, Inc., Cambridge, MA 02142, USA., Manoharan M; Alnylam Pharmaceuticals, Inc., Cambridge, MA 02142, USA., Brown D; MGH Program in Membrane Biology, Division of Nephrology, Massachusetts General Hospital and Harvard Medical School, Boston, MA 02114, USA., Maier MA; Alnylam Pharmaceuticals, Inc., Cambridge, MA 02142, USA., Jadhav V; Alnylam Pharmaceuticals, Inc., Cambridge, MA 02142, USA. |
| Source: | Nucleic acids research [Nucleic Acids Res] 2020 Dec 02; Vol. 48 (21), pp. 11827-11844. |
| Publication Type: | Journal Article; Research Support, Non-U.S. Gov't |
| Journal Info: | Publisher: Oxford University Press Country of Publication: England NLM ID: 0411011 Publication Model: Print Cited Medium: Internet ISSN: 1362-4962 (Electronic) Linking ISSN: 03051048 NLM ISO Abbreviation: Nucleic Acids Res Subsets: MEDLINE |
| Database: | MEDLINE Ultimate |
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| ISSN: | 1362-4962 |
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| DOI: | 10.1093/nar/gkaa670 |