Development of a dual hybrid AAV vector for endothelial-targeted expression of von Willebrand factor.

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Title: Development of a dual hybrid AAV vector for endothelial-targeted expression of von Willebrand factor.
Authors: Barbon E; Généthon, 91000, Evry, France.; Université Paris-Saclay, Université Evry, INSERM, Généthon, Integrare research unit UMR_S951, 91000, Evry, France., Kawecki C; Laboratory of Hemostasis, Inflammation and Thrombosis, Institut National de la Santé et de la Recherche Médicale UMR_1176, Université Paris-Saclay, 94276, Le Kremlin-Bicêtre, France., Marmier S; Généthon, 91000, Evry, France.; Université Paris-Saclay, Université Evry, INSERM, Généthon, Integrare research unit UMR_S951, 91000, Evry, France., Sakkal A; Généthon, 91000, Evry, France.; Université Paris-Saclay, Université Evry, INSERM, Généthon, Integrare research unit UMR_S951, 91000, Evry, France., Collaud F; Généthon, 91000, Evry, France.; Université Paris-Saclay, Université Evry, INSERM, Généthon, Integrare research unit UMR_S951, 91000, Evry, France., Charles S; Généthon, 91000, Evry, France.; Université Paris-Saclay, Université Evry, INSERM, Généthon, Integrare research unit UMR_S951, 91000, Evry, France., Ronzitti G; Généthon, 91000, Evry, France.; Université Paris-Saclay, Université Evry, INSERM, Généthon, Integrare research unit UMR_S951, 91000, Evry, France., Casari C; Laboratory of Hemostasis, Inflammation and Thrombosis, Institut National de la Santé et de la Recherche Médicale UMR_1176, Université Paris-Saclay, 94276, Le Kremlin-Bicêtre, France., Christophe OD; Laboratory of Hemostasis, Inflammation and Thrombosis, Institut National de la Santé et de la Recherche Médicale UMR_1176, Université Paris-Saclay, 94276, Le Kremlin-Bicêtre, France., Denis CV; Laboratory of Hemostasis, Inflammation and Thrombosis, Institut National de la Santé et de la Recherche Médicale UMR_1176, Université Paris-Saclay, 94276, Le Kremlin-Bicêtre, France., Lenting PJ; Laboratory of Hemostasis, Inflammation and Thrombosis, Institut National de la Santé et de la Recherche Médicale UMR_1176, Université Paris-Saclay, 94276, Le Kremlin-Bicêtre, France., Mingozzi F; Généthon, 91000, Evry, France. federico.mingozzi@sparktx.com.; Université Paris-Saclay, Université Evry, INSERM, Généthon, Integrare research unit UMR_S951, 91000, Evry, France. federico.mingozzi@sparktx.com.; Spark Therapeutics, Philadelphia, PA, 19103, USA. federico.mingozzi@sparktx.com.
Source: Gene therapy [Gene Ther] 2023 Apr; Vol. 30 (3-4), pp. 245-254. Date of Electronic Publication: 2021 Jan 17.
Publication Type: Journal Article; Research Support, Non-U.S. Gov't
Journal Info: Publisher: Nature Publishing Group Country of Publication: England NLM ID: 9421525 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1476-5462 (Electronic) Linking ISSN: 09697128 NLM ISO Abbreviation: Gene Ther Subsets: MEDLINE
Database: MEDLINE Ultimate
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  Data: Development of a dual hybrid AAV vector for endothelial-targeted expression of von Willebrand factor.
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  Data: <searchLink fieldCode="AU" term="%22Barbon+E%22">Barbon E</searchLink>; Généthon, 91000, Evry, France.; Université Paris-Saclay, Université Evry, INSERM, Généthon, Integrare research unit UMR_S951, 91000, Evry, France.<br /><searchLink fieldCode="AU" term="%22Kawecki+C%22">Kawecki C</searchLink>; Laboratory of Hemostasis, Inflammation and Thrombosis, Institut National de la Santé et de la Recherche Médicale UMR_1176, Université Paris-Saclay, 94276, Le Kremlin-Bicêtre, France.<br /><searchLink fieldCode="AU" term="%22Marmier+S%22">Marmier S</searchLink>; Généthon, 91000, Evry, France.; Université Paris-Saclay, Université Evry, INSERM, Généthon, Integrare research unit UMR_S951, 91000, Evry, France.<br /><searchLink fieldCode="AU" term="%22Sakkal+A%22">Sakkal A</searchLink>; Généthon, 91000, Evry, France.; Université Paris-Saclay, Université Evry, INSERM, Généthon, Integrare research unit UMR_S951, 91000, Evry, France.<br /><searchLink fieldCode="AU" term="%22Collaud+F%22">Collaud F</searchLink>; Généthon, 91000, Evry, France.; Université Paris-Saclay, Université Evry, INSERM, Généthon, Integrare research unit UMR_S951, 91000, Evry, France.<br /><searchLink fieldCode="AU" term="%22Charles+S%22">Charles S</searchLink>; Généthon, 91000, Evry, France.; Université Paris-Saclay, Université Evry, INSERM, Généthon, Integrare research unit UMR_S951, 91000, Evry, France.<br /><searchLink fieldCode="AU" term="%22Ronzitti+G%22">Ronzitti G</searchLink>; Généthon, 91000, Evry, France.; Université Paris-Saclay, Université Evry, INSERM, Généthon, Integrare research unit UMR_S951, 91000, Evry, France.<br /><searchLink fieldCode="AU" term="%22Casari+C%22">Casari C</searchLink>; Laboratory of Hemostasis, Inflammation and Thrombosis, Institut National de la Santé et de la Recherche Médicale UMR_1176, Université Paris-Saclay, 94276, Le Kremlin-Bicêtre, France.<br /><searchLink fieldCode="AU" term="%22Christophe+OD%22">Christophe OD</searchLink>; Laboratory of Hemostasis, Inflammation and Thrombosis, Institut National de la Santé et de la Recherche Médicale UMR_1176, Université Paris-Saclay, 94276, Le Kremlin-Bicêtre, France.<br /><searchLink fieldCode="AU" term="%22Denis+CV%22">Denis CV</searchLink>; Laboratory of Hemostasis, Inflammation and Thrombosis, Institut National de la Santé et de la Recherche Médicale UMR_1176, Université Paris-Saclay, 94276, Le Kremlin-Bicêtre, France.<br /><searchLink fieldCode="AU" term="%22Lenting+PJ%22">Lenting PJ</searchLink>; Laboratory of Hemostasis, Inflammation and Thrombosis, Institut National de la Santé et de la Recherche Médicale UMR_1176, Université Paris-Saclay, 94276, Le Kremlin-Bicêtre, France.<br /><searchLink fieldCode="AU" term="%22Mingozzi+F%22">Mingozzi F</searchLink>; Généthon, 91000, Evry, France. federico.mingozzi@sparktx.com.; Université Paris-Saclay, Université Evry, INSERM, Généthon, Integrare research unit UMR_S951, 91000, Evry, France. federico.mingozzi@sparktx.com.; Spark Therapeutics, Philadelphia, PA, 19103, USA. federico.mingozzi@sparktx.com.
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  Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22Nature+Publishing+Group%22">Nature Publishing Group </searchLink><i>Country of Publication: </i>England <i>NLM ID: </i>9421525 <i>Publication Model: </i>Print-Electronic <i>Cited Medium: </i>Internet <i>ISSN: </i>1476-5462 (Electronic) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2209697128%22">09697128 </searchLink><i>NLM ISO Abbreviation: </i>Gene Ther <i>Subsets: </i>MEDLINE
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