TorsinA restoration in a mouse model identifies a critical therapeutic window for DYT1 dystonia.

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Bibliographic Details
Title: TorsinA restoration in a mouse model identifies a critical therapeutic window for DYT1 dystonia.
Authors: Li J; Medical Scientist Training Program.; Cellular and Molecular Biology Graduate Program., Levin DS; Department of Neurology, University of Michigan, Ann Arbor, Michigan, USA., Kim AJ; Peter O'Donnell Jr. Brain Institute., Pappas SS; Peter O'Donnell Jr. Brain Institute.; Department of Neurology., Dauer WT; Peter O'Donnell Jr. Brain Institute.; Department of Neurology.; Department of Neuroscience, University of Texas Southwestern Medical Center, Dallas, Texas, USA.
Source: The Journal of clinical investigation [J Clin Invest] 2021 Mar 15; Vol. 131 (6).
Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't
Journal Info: Publisher: American Society for Clinical Investigation Country of Publication: United States NLM ID: 7802877 Publication Model: Print Cited Medium: Internet ISSN: 1558-8238 (Electronic) Linking ISSN: 00219738 NLM ISO Abbreviation: J Clin Invest Subsets: MEDLINE
Database: MEDLINE Ultimate
Description
ISSN:1558-8238
DOI:10.1172/JCI139606