TorsinA restoration in a mouse model identifies a critical therapeutic window for DYT1 dystonia.

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Title: TorsinA restoration in a mouse model identifies a critical therapeutic window for DYT1 dystonia.
Authors: Li J; Medical Scientist Training Program.; Cellular and Molecular Biology Graduate Program., Levin DS; Department of Neurology, University of Michigan, Ann Arbor, Michigan, USA., Kim AJ; Peter O'Donnell Jr. Brain Institute., Pappas SS; Peter O'Donnell Jr. Brain Institute.; Department of Neurology., Dauer WT; Peter O'Donnell Jr. Brain Institute.; Department of Neurology.; Department of Neuroscience, University of Texas Southwestern Medical Center, Dallas, Texas, USA.
Source: The Journal of clinical investigation [J Clin Invest] 2021 Mar 15; Vol. 131 (6).
Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't
Journal Info: Publisher: American Society for Clinical Investigation Country of Publication: United States NLM ID: 7802877 Publication Model: Print Cited Medium: Internet ISSN: 1558-8238 (Electronic) Linking ISSN: 00219738 NLM ISO Abbreviation: J Clin Invest Subsets: MEDLINE
Database: MEDLINE Ultimate
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  Data: <searchLink fieldCode="AU" term="%22Li+J%22">Li J</searchLink>; Medical Scientist Training Program.; Cellular and Molecular Biology Graduate Program.<br /><searchLink fieldCode="AU" term="%22Levin+DS%22">Levin DS</searchLink>; Department of Neurology, University of Michigan, Ann Arbor, Michigan, USA.<br /><searchLink fieldCode="AU" term="%22Kim+AJ%22">Kim AJ</searchLink>; Peter O'Donnell Jr. Brain Institute.<br /><searchLink fieldCode="AU" term="%22Pappas+SS%22">Pappas SS</searchLink>; Peter O'Donnell Jr. Brain Institute.; Department of Neurology.<br /><searchLink fieldCode="AU" term="%22Dauer+WT%22">Dauer WT</searchLink>; Peter O'Donnell Jr. Brain Institute.; Department of Neurology.; Department of Neuroscience, University of Texas Southwestern Medical Center, Dallas, Texas, USA.
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  Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22American+Society+for+Clinical+Investigation%22">American Society for Clinical Investigation </searchLink><i>Country of Publication: </i>United States <i>NLM ID: </i>7802877 <i>Publication Model: </i>Print <i>Cited Medium: </i>Internet <i>ISSN: </i>1558-8238 (Electronic) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2200219738%22">00219738 </searchLink><i>NLM ISO Abbreviation: </i>J Clin Invest <i>Subsets: </i>MEDLINE
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        Value: 10.1172/JCI139606
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      – TitleFull: TorsinA restoration in a mouse model identifies a critical therapeutic window for DYT1 dystonia.
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              Text: 2021 Mar 15
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