Integrative chemogenomic analysis identifies small molecules that partially rescue ΔF508-CFTR for cystic fibrosis.
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| Title: | Integrative chemogenomic analysis identifies small molecules that partially rescue ΔF508-CFTR for cystic fibrosis. |
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| Authors: | Hodos RA; Institute for Next Generation Healthcare, Mount Sinai School of Medicine, New York, NY, USA.; Courant Institute for Mathematical Sciences, New York University, New York, NY, USA., Strub MD; Department of Pediatrics, University of Iowa, Carver College of Medicine, Iowa City, IA, USA.; Interdisciplinary Graduate Program in Genetics, University of Iowa, Iowa City, IA, USA., Ramachandran S; Editas Medicine, Cambridge, MA, USA., Meleshkevitch EA; Department of Physiology and Biophysics, Rosalind Franklin University, North Chicago, IL, USA., Boudko DY; Department of Physiology and Biophysics, Rosalind Franklin University, North Chicago, IL, USA., Bridges RJ; Department of Physiology and Biophysics, Rosalind Franklin University, North Chicago, IL, USA., Dudley JT; Institute for Next Generation Healthcare, Mount Sinai School of Medicine, New York, NY, USA., McCray PB Jr; Department of Pediatrics, University of Iowa, Carver College of Medicine, Iowa City, IA, USA.; Interdisciplinary Graduate Program in Genetics, University of Iowa, Iowa City, IA, USA. |
| Source: | CPT: pharmacometrics & systems pharmacology [CPT Pharmacometrics Syst Pharmacol] 2021 May; Vol. 10 (5), pp. 500-510. Date of Electronic Publication: 2021 May 02. |
| Publication Type: | Journal Article; Research Support, N.I.H., Extramural |
| Journal Info: | Publisher: Wiley Country of Publication: United States NLM ID: 101580011 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 2163-8306 (Electronic) Linking ISSN: 21638306 NLM ISO Abbreviation: CPT Pharmacometrics Syst Pharmacol Subsets: MEDLINE |
| Database: | MEDLINE Ultimate |
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| ISSN: | 2163-8306 |
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| DOI: | 10.1002/psp4.12626 |