Mesyl Phosphoramidate Oligonucleotides as Potential Splice-Switching Agents: Impact of Backbone Structure on Activity and Intracellular Localization.

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Title: Mesyl Phosphoramidate Oligonucleotides as Potential Splice-Switching Agents: Impact of Backbone Structure on Activity and Intracellular Localization.
Authors: Hammond SM; Department of Paediatrics and Anatomy and Genetics, University of Oxford, Oxford, United Kingdom., Sergeeva OV; Center of Life Sciences, Skolkovo Institute of Science and Technology, Moscow, Russia., Melnikov PA; Serbsky National Medical Research Center for Psychiatry and Narcology, Moscow, Russia., Goli L; Department of Physiology, Anatomy and Genetics, University of Oxford, Oxford, United Kingdom., Stoodley J; Department of Paediatrics and Anatomy and Genetics, University of Oxford, Oxford, United Kingdom., Zatsepin TS; Center of Life Sciences, Skolkovo Institute of Science and Technology, Moscow, Russia.; Faculty of Chemistry, Lomonosov Moscow State University, Moscow, Russia., Stetsenko DA; Department of Physics, Novosibirsk State University, Novosibirsk, Russia.; Institute of Cytology and Genetics, Siberian Branch of the Russian Academy of Sciences, Novosibirsk, Russia., Wood MJA; Department of Paediatrics and Anatomy and Genetics, University of Oxford, Oxford, United Kingdom.
Source: Nucleic acid therapeutics [Nucleic Acid Ther] 2021 Jun; Vol. 31 (3), pp. 190-200. Date of Electronic Publication: 2021 May 14.
Publication Type: Journal Article; Research Support, Non-U.S. Gov't
Journal Info: Publisher: Mary Ann Liebert, Inc Country of Publication: United States NLM ID: 101562758 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 2159-3345 (Electronic) Linking ISSN: 21593337 NLM ISO Abbreviation: Nucleic Acid Ther Subsets: MEDLINE
Database: MEDLINE Ultimate
Description
ISSN:2159-3345
DOI:10.1089/nat.2020.0860