Current neurologic treatment and emerging therapies in CDKL5 deficiency disorder.

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Title: Current neurologic treatment and emerging therapies in CDKL5 deficiency disorder.
Authors: Olson HE; Division of Epilepsy and Clinical Neurophysiology, Department of Neurology, Boston Children's Hospital, 300 Longwood Avenue, Mailstop 3063, Boston, MA, 02115, USA. Heather.Olson@childrens.harvard.edu., Daniels CI; Division of Epilepsy and Clinical Neurophysiology, Department of Neurology, Boston Children's Hospital, 300 Longwood Avenue, Mailstop 3063, Boston, MA, 02115, USA., Haviland I; Division of Epilepsy and Clinical Neurophysiology, Department of Neurology, Boston Children's Hospital, 300 Longwood Avenue, Mailstop 3063, Boston, MA, 02115, USA., Swanson LC; Division of Epilepsy and Clinical Neurophysiology, Department of Neurology, Boston Children's Hospital, 300 Longwood Avenue, Mailstop 3063, Boston, MA, 02115, USA., Greene CA; Division of Epilepsy and Clinical Neurophysiology, Department of Neurology, Boston Children's Hospital, 300 Longwood Avenue, Mailstop 3063, Boston, MA, 02115, USA., Denny AMM; Division of Epilepsy and Clinical Neurophysiology, Department of Neurology, Boston Children's Hospital, 300 Longwood Avenue, Mailstop 3063, Boston, MA, 02115, USA.; Division of Pediatric Neurology, University of Saskatchewan, Saskatoon, SK, Canada., Demarest ST; Children's Hospital Colorado, University of Colorado, School of Medicine, Aurora, CO, USA.; Department of Pediatrics, School of Medicine, University of Colorado, Aurora, CO, USA., Pestana-Knight E; Epilepsy Center, Neurological Institute, Cleveland Clinic, Cleveland, OH, USA., Zhang X; Epilepsy Center, Neurological Institute, Cleveland Clinic, Cleveland, OH, USA., Moosa AN; Epilepsy Center, Neurological Institute, Cleveland Clinic, Cleveland, OH, USA., Fidell A; Children's Hospital Colorado, University of Colorado, School of Medicine, Aurora, CO, USA.; Department of Pediatrics, School of Medicine, University of Colorado, Aurora, CO, USA., Weisenberg JL; Department of Pediatric Neurology, Washington University School of Medicine, St. Louis, MO, USA., Suter B; Division of Child Neurology, Texas Children's Hospital, Departments of Neurology and Pediatrics, Baylor College of Medicine, Houston, TX, USA., Fu C; Department of Pediatrics, Vanderbilt University Medical Center, Nashville, TN, USA., Neul JL; Department of Pediatrics, Vanderbilt University Medical Center, Nashville, TN, USA., Percy AK; Department of Pediatrics, University of Alabama at Birmingham, Birmingham, AL, USA., Marsh ED; Division of Child Neurology, Children's Hospital of Philadelphia, Departments of Neurology and Pediatrics, Perelman School of Medicine, University of Pennsylvania, Philadelphia, PA, USA., Benke TA; Children's Hospital Colorado, University of Colorado, School of Medicine, Aurora, CO, USA.; Department of Pediatrics, School of Medicine, University of Colorado, Aurora, CO, USA.; Departments of Pharmacology, Neurology, and Otolaryngology, School of Medicine, University of Colorado, Aurora, CO, USA., Poduri A; Division of Epilepsy and Clinical Neurophysiology, Department of Neurology, Boston Children's Hospital, 300 Longwood Avenue, Mailstop 3063, Boston, MA, 02115, USA.
Source: Journal of neurodevelopmental disorders [J Neurodev Disord] 2021 Sep 16; Vol. 13 (1), pp. 40. Date of Electronic Publication: 2021 Sep 16.
Publication Type: Journal Article; Research Support, N.I.H., Extramural
Journal Info: Publisher: BioMed Central Country of Publication: England NLM ID: 101483832 Publication Model: Electronic Cited Medium: Internet ISSN: 1866-1955 (Electronic) Linking ISSN: 18661947 NLM ISO Abbreviation: J Neurodev Disord Subsets: MEDLINE
Database: MEDLINE Ultimate
Description
ISSN:1866-1955
DOI:10.1186/s11689-021-09384-z