Chimeric Mice Engrafted With Canine Hepatocytes Exhibits Similar AAV Transduction Efficiency to Hemophilia B Dog.

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Title: Chimeric Mice Engrafted With Canine Hepatocytes Exhibits Similar AAV Transduction Efficiency to Hemophilia B Dog.
Authors: Shao W; Academy of Medical Engineering and Translational Medicine, Tianjin University, Tianjin, China.; Gene Therapy Center, University of North Carolina at Chapel Hill, Chapel Hill, NC, United States., Sun J; Gene Therapy Center, University of North Carolina at Chapel Hill, Chapel Hill, NC, United States.; Division of Pharmacoengineering and Molecular Pharmaceutics, Eshelman School of Pharmacy, University of North Carolina at Chapel Hill, Chapel Hill, NC, United States., Chen X; Gene Therapy Center, University of North Carolina at Chapel Hill, Chapel Hill, NC, United States., Dobbins A; Gene Therapy Center, University of North Carolina at Chapel Hill, Chapel Hill, NC, United States., Merricks EP; Department of Pathology and Laboratory Medicine and The Blood Research Center, University of North Carolina at Chapel Hill, Chapel Hill, NC, United States., Samulski RJ; Gene Therapy Center, University of North Carolina at Chapel Hill, Chapel Hill, NC, United States.; Department of Pharmacology, School of Medicine, University of North Carolina at Chapel Hill, Chapel Hill, NC, United States., Nichols TC; Department of Pathology and Laboratory Medicine and The Blood Research Center, University of North Carolina at Chapel Hill, Chapel Hill, NC, United States., Li C; Gene Therapy Center, University of North Carolina at Chapel Hill, Chapel Hill, NC, United States.; Department of Pediatrics, University of North Carolina at Chapel Hill, Chapel Hill, NC, United States.; Carolina Institute for Developmental Disabilities, University of North Carolina at Chapel Hill, Chapel Hill, NC, United States.
Source: Frontiers in pharmacology [Front Pharmacol] 2022 Jan 31; Vol. 13, pp. 815317. Date of Electronic Publication: 2022 Jan 31 (Print Publication: 2022).
Publication Type: Journal Article
Journal Info: Publisher: Frontiers Media] Country of Publication: Switzerland NLM ID: 101548923 Publication Model: eCollection Cited Medium: Print ISSN: 1663-9812 (Print) Linking ISSN: 16639812 NLM ISO Abbreviation: Front Pharmacol Subsets: PubMed not MEDLINE
Database: MEDLINE Ultimate
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Description
ISSN:1663-9812
DOI:10.3389/fphar.2022.815317