ePHex: a phase 3, double-blind, placebo-controlled, randomized study to evaluate long-term efficacy and safety of Oxalobacter formigenes in patients with primary hyperoxaluria.

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Title: ePHex: a phase 3, double-blind, placebo-controlled, randomized study to evaluate long-term efficacy and safety of Oxalobacter formigenes in patients with primary hyperoxaluria.
Authors: Ariceta G; Hospital Vall d'Hebron, Barcelona, Spain. gariceta@vhebron.net., Collard L; Centre Hospitalier Umniversitaire de Liege, Liege, Belgium., Abroug S; Hôpital Universitaire Sahloul, Sousse, Tunisia., Moochhala SH; Royal Free Hospital, London, UK., Gould E; Vanderbilt University Hospital, Nashville, USA., Boussetta A; Charles Nicolle University Hospital, Tunis, Tunisia., Ben Hmida M; Hedi Chaker University Hospital, Sfax, Tunisia., De S; Nottingham Children's Hospital, Nottingham, UK., Hunley TE; Vanderbilt University Hospital, Nashville, USA., Jarraya F; Hedi Chaker University Hospital, Sfax, Tunisia., Fraga G; Hospital Vall d'Hebron, Barcelona, Spain.; Hospital Sant Pau, Barcelona, Spain., Banos A; OxThera Intellectual Property AB, Stockholm, Sweden., Lindner E; OxThera Intellectual Property AB, Stockholm, Sweden., Dehmel B; OxThera Intellectual Property AB, Stockholm, Sweden., Schalk G; Kindernierenzentrum, Bonn, Germany.
Source: Pediatric nephrology (Berlin, Germany) [Pediatr Nephrol] 2023 Feb; Vol. 38 (2), pp. 403-415. Date of Electronic Publication: 2022 May 12.
Publication Type: Randomized Controlled Trial; Clinical Trial, Phase III; Journal Article; Research Support, Non-U.S. Gov't
Journal Info: Publisher: Springer International Country of Publication: Germany NLM ID: 8708728 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1432-198X (Electronic) Linking ISSN: 0931041X NLM ISO Abbreviation: Pediatr Nephrol Subsets: MEDLINE
Database: MEDLINE Ultimate
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ISSN:1432-198X
DOI:10.1007/s00467-022-05591-5