Potential CRISPR Base Editing Therapeutic Options in a Sorsby Fundus Dystrophy Patient.
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| Title: | Potential CRISPR Base Editing Therapeutic Options in a Sorsby Fundus Dystrophy Patient. |
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| Authors: | Elsayed MEAA; Oxford Eye Hospital, Oxford University Hospitals NHS Foundation Trust, Oxford OX3 9DU, UK., Kaukonen M; Oxford Eye Hospital, Oxford University Hospitals NHS Foundation Trust, Oxford OX3 9DU, UK.; Nuffield Department of Clinical Neuroscience, University of Oxford, Oxford OX3 9DU, UK., Kiraly P; Oxford Eye Hospital, Oxford University Hospitals NHS Foundation Trust, Oxford OX3 9DU, UK., Kapetanovic JC; Oxford Eye Hospital, Oxford University Hospitals NHS Foundation Trust, Oxford OX3 9DU, UK.; Nuffield Department of Clinical Neuroscience, University of Oxford, Oxford OX3 9DU, UK., MacLaren RE; Oxford Eye Hospital, Oxford University Hospitals NHS Foundation Trust, Oxford OX3 9DU, UK.; Nuffield Department of Clinical Neuroscience, University of Oxford, Oxford OX3 9DU, UK. |
| Source: | Genes [Genes (Basel)] 2022 Nov 12; Vol. 13 (11). Date of Electronic Publication: 2022 Nov 12. |
| Publication Type: | Case Reports; Journal Article; Research Support, Non-U.S. Gov't |
| Journal Info: | Publisher: MDPI Country of Publication: Switzerland NLM ID: 101551097 Publication Model: Electronic Cited Medium: Internet ISSN: 2073-4425 (Electronic) Linking ISSN: 20734425 NLM ISO Abbreviation: Genes (Basel) Subsets: MEDLINE |
| Database: | MEDLINE Ultimate |
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