Natural history of cardiac findings in mucopolysaccharidosis type I: report from an international registry.
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| Title: | Natural history of cardiac findings in mucopolysaccharidosis type I: report from an international registry. |
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| Authors: | Braunlin E; Department of Pediatrics, University of Minnesota, Minneapolis, MN, USA., Bay L; Hospital Nacional de Pediatría J. P. Garrahan, Ciudad Autónoma de Buenos Aires, Buenos Aires, Argentina., Guffon N; Centre de Référence des Maladies Héréditaires du Métabolisme, Hôpital Femme Mère Enfant, Lyon, France., Yang M; Formerly Epidemiology and Biostatistics, Sanofi, Cambridge, MA, USA., Pangaud N; Cardiology, Louis Pradel Hospital, Hospices Civils de Lyon, Lyon, France., Clarke LA; Department of Medical Genetics and the British Columbia Children's Hospital Research Institute, University of British Columbia, Vancouver, BC, Canada. |
| Source: | Cardiology in the young [Cardiol Young] 2024 Feb; Vol. 34 (2), pp. 401-411. Date of Electronic Publication: 2023 Oct 18. |
| Publication Type: | Journal Article |
| Journal Info: | Publisher: Cambridge University Press Country of Publication: England NLM ID: 9200019 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1467-1107 (Electronic) Linking ISSN: 10479511 NLM ISO Abbreviation: Cardiol Young Subsets: MEDLINE |
| Database: | MEDLINE Ultimate |
| ISSN: | 1467-1107 |
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| DOI: | 10.1017/S1047951123003347 |