Continued safety and long-term effectiveness of onasemnogene abeparvovec in Ohio.

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Title: Continued safety and long-term effectiveness of onasemnogene abeparvovec in Ohio.
Authors: Waldrop MA; Center for Gene Therapy, Abigail Wexner Research Institute, Nationwide Children's Hospital, Columbus OH, 43205, USA; Departments of Pediatrics and Neurology, Ohio State University Wexner Medical Center, Columbus OH, 43205, USA. Electronic address: megan.waldrop@nationwidechildrens.org., Chagat S; Department of Neurology, Nationwide Children's Hospital, Columbus, OH 43205, USA., Storey M; Department of Pharmacy, Nationwide Children's Hospital, Columbus, OH 43205, USA., Meyer A; Center for Gene Therapy, Abigail Wexner Research Institute, Nationwide Children's Hospital, Columbus OH, 43205, USA., Iammarino M; Center for Gene Therapy, Abigail Wexner Research Institute, Nationwide Children's Hospital, Columbus OH, 43205, USA., Reash N; Center for Gene Therapy, Abigail Wexner Research Institute, Nationwide Children's Hospital, Columbus OH, 43205, USA., Alfano L; Center for Gene Therapy, Abigail Wexner Research Institute, Nationwide Children's Hospital, Columbus OH, 43205, USA., Lowes L; Center for Gene Therapy, Abigail Wexner Research Institute, Nationwide Children's Hospital, Columbus OH, 43205, USA., Noritz G; Department of Pediatrics, Nationwide Children's hospital, Columbus, OH 43205, USA., Prochoroff A; Department of Pediatric Neurology, Metro Health, Cleveland OH, USA., Rossman I; Department of Pediatric Neurology, Akron Children's Hospital, Akron OH, USA., Ginsberg M; Department of Pediatric Neurology, Akron Children's Hospital, Akron OH, USA., Mosher K; Department of Pediatric Physiatry, Akron Children's Hospital, Akron OH, USA., Broomall E; Department of Pediatric Neurology, Cincinnati Children's Hospital Medical Center, Cincinnati OH, USA., Bass N; Division of Pediatric Neurology, Department of Pediatrics, Rainbow Babies and Children's Hospital, Cleveland OH, USA., Gushue C; Departments of Pediatrics and Pulmonology, Ohio State University Wexner Medical Center, Columbus OH 43205, USA., Kotha K; Departments of Pediatrics and Pulmonology, Ohio State University Wexner Medical Center, Columbus OH 43205, USA., Paul G; Departments of Pediatrics and Pulmonology, Ohio State University Wexner Medical Center, Columbus OH 43205, USA., Shell R; Departments of Pediatrics and Pulmonology, Ohio State University Wexner Medical Center, Columbus OH 43205, USA., Tsao CY; Departments of Pediatrics and Neurology, Ohio State University Wexner Medical Center, Columbus OH, 43205, USA., Mendell JR; Center for Gene Therapy, Abigail Wexner Research Institute, Nationwide Children's Hospital, Columbus OH, 43205, USA; Departments of Pediatrics and Neurology, Ohio State University Wexner Medical Center, Columbus OH, 43205, USA., Connolly AM; Center for Gene Therapy, Abigail Wexner Research Institute, Nationwide Children's Hospital, Columbus OH, 43205, USA; Departments of Pediatrics and Neurology, Ohio State University Wexner Medical Center, Columbus OH, 43205, USA.
Source: Neuromuscular disorders : NMD [Neuromuscul Disord] 2024 Jan; Vol. 34, pp. 41-48. Date of Electronic Publication: 2023 Dec 02.
Publication Type: Journal Article
Journal Info: Publisher: Pergamon Press Country of Publication: England NLM ID: 9111470 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1873-2364 (Electronic) Linking ISSN: 09608966 NLM ISO Abbreviation: Neuromuscul Disord Subsets: MEDLINE
Database: MEDLINE Ultimate
Description
ISSN:1873-2364
DOI:10.1016/j.nmd.2023.11.010