Burosumab vs conventional therapy in children with X-linked hypophosphatemia: results of the open-label, phase 3 extension period.
Saved in:
| Title: | Burosumab vs conventional therapy in children with X-linked hypophosphatemia: results of the open-label, phase 3 extension period. |
|---|---|
| Authors: | Ward LM; Department of Pediatrics, Faculty of Medicine, University of Ottawa, Ottawa, Ontario, K1H 8L1, Canada., Högler W; Department of Paediatrics and Adolescent Medicine, Johannes Kepler University Linz, 4040 Linz, Austria.; Institute of Metabolism and Systems Research, University of Birmingham, Edgbaston, Birmingham, B15 2TT, United Kingdom., Glorieux FH; Department of Surgery, Pediatrics, and Human Genetics, Shriners Hospitals for Children and McGill University, Montreal, Quebec, H4A 0A9, Canada., Portale AA; Department of Pediatrics, University of California, San Francisco, CA, 94158, United States., Whyte MP; Shriners Hospitals for Children St Louis, St Louis, MO, 63110, United States., Munns CF; Faculty of Medicine, The University of Queensland, Brisbane, Queensland, 4072, Australia.; Faculty of Medicine, Child Health Research Centre, The University of Queensland, Brisbane, Queensland, 4072, Australia.; Department of Endocrinology and Diabetes, Queensland Children's Hospital, Brisbane, Queensland, 4072, Australia., Nilsson O; Division of Pediatric Endocrinology, Department of Women's and Children's Health, Center for Molecular Medicine, Karolinska Institutet and University Hospital, SE-17176 Stockholm, Sweden.; Department of Pediatrics, School of Medical Sciences, Örebro University and University Hospital, S-701 82 Örebro, Sweden., Simmons JH; Division of Endocrinology and Diabetes, Department of Pediatrics, Vanderbilt University School of Medicine, Vanderbilt University, Nashville, TN, 37232, United States., Padidela R; Department of Paediatric Endocrinology, Royal Manchester Children's Hospital, Manchester, M13 9WL, United Kingdom., Namba N; Department of Pediatrics, Osaka Hospital, Japan Community Healthcare Organization, Osaka, 553-0003, Japan.; Osaka University Graduate School of Medicine, Osaka, 565-0871, Japan., Cheong HI; Department of Pediatrics, Hallym University Sacred Heart Hospital, Dongan-gu, Anyang, 14068, South Korea., Sochett E; Department of Pediatrics, Hospital for Sick Children, Toronto, Ontario, M5G 1E8, Canada., Muroya K; Department of Endocrinology, Kanagawa Children's Medical Center, Yokohama, Kanagawa 232-0066, Japan., Tanaka H; Division of Pediatrics, Okayama Saiseikai General Hospital Outpatient Center, Kita-ku, Okayama, 700-8511, Japan., Pitukcheewanont P; Center of Endocrinology, Diabetes and Metabolism, Children's Hospital of Los Angeles, Los Angeles, CA, 90027, United States., Gottesman GS; Shriners Hospitals for Children St Louis, St Louis, MO, 63110, United States., Biggin A; Department of Endocrinology, The University of Sydney Children's Hospital Westmead Clinical School, The Children's Hospital at Westmead, Westmead, New South Wales, 2145, Australia., Perwad F; Department of Pediatrics, University of California, San Francisco, CA, 94158, United States., Chen A; Ultragenyx Pharmaceutical Inc., Novato, CA, 94949, United States., Lawrence Merritt Ii J; Ultragenyx Pharmaceutical Inc., Novato, CA, 94949, United States., Imel EA; Department of Medicine, Indiana University School of Medicine, Indianapolis, IN, 46202, United States. |
| Source: | JBMR plus [JBMR Plus] 2024 Jan 04; Vol. 8 (1), pp. ziad001. Date of Electronic Publication: 2024 Jan 04 (Print Publication: 2024). |
| Publication Type: | Clinical Trial; Journal Article |
| Journal Info: | Publisher: Oxford University Press Country of Publication: England NLM ID: 101707013 Publication Model: eCollection Cited Medium: Internet ISSN: 2473-4039 (Electronic) Linking ISSN: 24734039 NLM ISO Abbreviation: JBMR Plus Subsets: PubMed not MEDLINE |
| Database: | MEDLINE Ultimate |
|
Full text is not displayed to guests.
Login for full access.
|
|
| ISSN: | 2473-4039 |
|---|---|
| DOI: | 10.1093/jbmrpl/ziad001 |