Long-Term Comparative Efficacy and Safety of Risdiplam and Nusinersen in Children with Type 1 Spinal Muscular Atrophy.
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| Title: | Long-Term Comparative Efficacy and Safety of Risdiplam and Nusinersen in Children with Type 1 Spinal Muscular Atrophy. |
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| Authors: | Kokaliaris C; F. Hoffmann-La Roche Ltd, Grenzacherstrasse 124, 4070, Basel, Switzerland. christos.kokaliaris@roche.com., Evans R; Visible Analytics, Oxford, UK., Hawkins N; Visible Analytics, Oxford, UK.; Institute of Health & Wellbeing, University of Glasgow, Glasgow, UK., Mahajan A; Bridge Medical Consulting Ltd, London, UK., Scott DA; Visible Analytics, Oxford, UK., Sutherland CS; F. Hoffmann-La Roche Ltd, Grenzacherstrasse 124, 4070, Basel, Switzerland., Nam J; F. Hoffmann-La Roche Ltd, Grenzacherstrasse 124, 4070, Basel, Switzerland., Sajeev G; Analysis Group, Inc, Boston, MA, USA. |
| Source: | Advances in therapy [Adv Ther] 2024 Jun; Vol. 41 (6), pp. 2414-2434. Date of Electronic Publication: 2024 May 05. |
| Publication Type: | Journal Article; Comparative Study; Research Support, Non-U.S. Gov't |
| Journal Info: | Publisher: Health Communications Inc Country of Publication: United States NLM ID: 8611864 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1865-8652 (Electronic) Linking ISSN: 0741238X NLM ISO Abbreviation: Adv Ther Subsets: MEDLINE |
| Database: | MEDLINE Ultimate |
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| ISSN: | 1865-8652 |
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| DOI: | 10.1007/s12325-024-02845-6 |
