In vivo genome editing via CRISPR/Cas9-mediated homology-independent targeted integration for Bietti crystalline corneoretinal dystrophy treatment.

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Title: In vivo genome editing via CRISPR/Cas9-mediated homology-independent targeted integration for Bietti crystalline corneoretinal dystrophy treatment.
Authors: Meng X; Department of Ophthalmology, Third Hospital, Peking University, Beijing, China.; Beijing Key Laboratory of Restoration of Damaged Ocular Nerve, Peking University Third Hospital, Beijing, China., Jia R; Department of Ophthalmology, Third Hospital, Peking University, Beijing, China.; Beijing Key Laboratory of Restoration of Damaged Ocular Nerve, Peking University Third Hospital, Beijing, China., Zhao X; Beijing Chinagene Co., LTD, Beijing, China., Zhang F; Beijing Chinagene Co., LTD, Beijing, China., Chen S; Beijing Chinagene Co., LTD, Beijing, China., Yu S; Department of Ophthalmology, Third Hospital, Peking University, Beijing, China.; Beijing Key Laboratory of Restoration of Damaged Ocular Nerve, Peking University Third Hospital, Beijing, China., Liu X; Department of Ophthalmology, Third Hospital, Peking University, Beijing, China.; Beijing Key Laboratory of Restoration of Damaged Ocular Nerve, Peking University Third Hospital, Beijing, China., Dou H; Department of Ophthalmology, Third Hospital, Peking University, Beijing, China.; Beijing Key Laboratory of Restoration of Damaged Ocular Nerve, Peking University Third Hospital, Beijing, China., Feng X; Department of Ophthalmology, Third Hospital, Peking University, Beijing, China.; Beijing Key Laboratory of Restoration of Damaged Ocular Nerve, Peking University Third Hospital, Beijing, China., Zhang J; Beijing Chinagene Co., LTD, Beijing, China., Wang N; Beijing Chinagene Co., LTD, Beijing, China., Xu B; Department of Ophthalmology, Third Hospital, Peking University, Beijing, China.; Beijing Key Laboratory of Restoration of Damaged Ocular Nerve, Peking University Third Hospital, Beijing, China., Yang L; Department of Ophthalmology, Third Hospital, Peking University, Beijing, China. alexlipingyang@bjmu.edu.cn.; Beijing Key Laboratory of Restoration of Damaged Ocular Nerve, Peking University Third Hospital, Beijing, China. alexlipingyang@bjmu.edu.cn.
Source: Nature communications [Nat Commun] 2024 May 06; Vol. 15 (1), pp. 3773. Date of Electronic Publication: 2024 May 06.
Publication Type: Journal Article; Research Support, Non-U.S. Gov't
Journal Info: Publisher: Nature Pub. Group Country of Publication: England NLM ID: 101528555 Publication Model: Electronic Cited Medium: Internet ISSN: 2041-1723 (Electronic) Linking ISSN: 20411723 NLM ISO Abbreviation: Nat Commun Subsets: MEDLINE
Database: MEDLINE Ultimate
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ISSN:2041-1723
DOI:10.1038/s41467-024-48092-9