In vivo genome editing via CRISPR/Cas9-mediated homology-independent targeted integration for Bietti crystalline corneoretinal dystrophy treatment.
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| Title: | In vivo genome editing via CRISPR/Cas9-mediated homology-independent targeted integration for Bietti crystalline corneoretinal dystrophy treatment. |
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| Authors: | Meng X; Department of Ophthalmology, Third Hospital, Peking University, Beijing, China.; Beijing Key Laboratory of Restoration of Damaged Ocular Nerve, Peking University Third Hospital, Beijing, China., Jia R; Department of Ophthalmology, Third Hospital, Peking University, Beijing, China.; Beijing Key Laboratory of Restoration of Damaged Ocular Nerve, Peking University Third Hospital, Beijing, China., Zhao X; Beijing Chinagene Co., LTD, Beijing, China., Zhang F; Beijing Chinagene Co., LTD, Beijing, China., Chen S; Beijing Chinagene Co., LTD, Beijing, China., Yu S; Department of Ophthalmology, Third Hospital, Peking University, Beijing, China.; Beijing Key Laboratory of Restoration of Damaged Ocular Nerve, Peking University Third Hospital, Beijing, China., Liu X; Department of Ophthalmology, Third Hospital, Peking University, Beijing, China.; Beijing Key Laboratory of Restoration of Damaged Ocular Nerve, Peking University Third Hospital, Beijing, China., Dou H; Department of Ophthalmology, Third Hospital, Peking University, Beijing, China.; Beijing Key Laboratory of Restoration of Damaged Ocular Nerve, Peking University Third Hospital, Beijing, China., Feng X; Department of Ophthalmology, Third Hospital, Peking University, Beijing, China.; Beijing Key Laboratory of Restoration of Damaged Ocular Nerve, Peking University Third Hospital, Beijing, China., Zhang J; Beijing Chinagene Co., LTD, Beijing, China., Wang N; Beijing Chinagene Co., LTD, Beijing, China., Xu B; Department of Ophthalmology, Third Hospital, Peking University, Beijing, China.; Beijing Key Laboratory of Restoration of Damaged Ocular Nerve, Peking University Third Hospital, Beijing, China., Yang L; Department of Ophthalmology, Third Hospital, Peking University, Beijing, China. alexlipingyang@bjmu.edu.cn.; Beijing Key Laboratory of Restoration of Damaged Ocular Nerve, Peking University Third Hospital, Beijing, China. alexlipingyang@bjmu.edu.cn. |
| Source: | Nature communications [Nat Commun] 2024 May 06; Vol. 15 (1), pp. 3773. Date of Electronic Publication: 2024 May 06. |
| Publication Type: | Journal Article; Research Support, Non-U.S. Gov't |
| Journal Info: | Publisher: Nature Pub. Group Country of Publication: England NLM ID: 101528555 Publication Model: Electronic Cited Medium: Internet ISSN: 2041-1723 (Electronic) Linking ISSN: 20411723 NLM ISO Abbreviation: Nat Commun Subsets: MEDLINE |
| Database: | MEDLINE Ultimate |
| FullText | Text: Availability: 0 |
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| Header | DbId: mdl DbLabel: MEDLINE Ultimate An: 38710738 AccessLevel: 2 PubType: Academic Journal PubTypeId: academicJournal PreciseRelevancyScore: 0 |
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| Items | – Name: Title Label: Title Group: Ti Data: In vivo genome editing via CRISPR/Cas9-mediated homology-independent targeted integration for Bietti crystalline corneoretinal dystrophy treatment. – Name: Author Label: Authors Group: Au Data: <searchLink fieldCode="AU" term="%22Meng+X%22">Meng X</searchLink>; Department of Ophthalmology, Third Hospital, Peking University, Beijing, China.; Beijing Key Laboratory of Restoration of Damaged Ocular Nerve, Peking University Third Hospital, Beijing, China.<br /><searchLink fieldCode="AU" term="%22Jia+R%22">Jia R</searchLink>; Department of Ophthalmology, Third Hospital, Peking University, Beijing, China.; Beijing Key Laboratory of Restoration of Damaged Ocular Nerve, Peking University Third Hospital, Beijing, China.<br /><searchLink fieldCode="AU" term="%22Zhao+X%22">Zhao X</searchLink>; Beijing Chinagene Co., LTD, Beijing, China.<br /><searchLink fieldCode="AU" term="%22Zhang+F%22">Zhang F</searchLink>; Beijing Chinagene Co., LTD, Beijing, China.<br /><searchLink fieldCode="AU" term="%22Chen+S%22">Chen S</searchLink>; Beijing Chinagene Co., LTD, Beijing, China.<br /><searchLink fieldCode="AU" term="%22Yu+S%22">Yu S</searchLink>; Department of Ophthalmology, Third Hospital, Peking University, Beijing, China.; Beijing Key Laboratory of Restoration of Damaged Ocular Nerve, Peking University Third Hospital, Beijing, China.<br /><searchLink fieldCode="AU" term="%22Liu+X%22">Liu X</searchLink>; Department of Ophthalmology, Third Hospital, Peking University, Beijing, China.; Beijing Key Laboratory of Restoration of Damaged Ocular Nerve, Peking University Third Hospital, Beijing, China.<br /><searchLink fieldCode="AU" term="%22Dou+H%22">Dou H</searchLink>; Department of Ophthalmology, Third Hospital, Peking University, Beijing, China.; Beijing Key Laboratory of Restoration of Damaged Ocular Nerve, Peking University Third Hospital, Beijing, China.<br /><searchLink fieldCode="AU" term="%22Feng+X%22">Feng X</searchLink>; Department of Ophthalmology, Third Hospital, Peking University, Beijing, China.; Beijing Key Laboratory of Restoration of Damaged Ocular Nerve, Peking University Third Hospital, Beijing, China.<br /><searchLink fieldCode="AU" term="%22Zhang+J%22">Zhang J</searchLink>; Beijing Chinagene Co., LTD, Beijing, China.<br /><searchLink fieldCode="AU" term="%22Wang+N%22">Wang N</searchLink>; Beijing Chinagene Co., LTD, Beijing, China.<br /><searchLink fieldCode="AU" term="%22Xu+B%22">Xu B</searchLink>; Department of Ophthalmology, Third Hospital, Peking University, Beijing, China.; Beijing Key Laboratory of Restoration of Damaged Ocular Nerve, Peking University Third Hospital, Beijing, China.<br /><searchLink fieldCode="AU" term="%22Yang+L%22">Yang L</searchLink>; Department of Ophthalmology, Third Hospital, Peking University, Beijing, China. alexlipingyang@bjmu.edu.cn.; Beijing Key Laboratory of Restoration of Damaged Ocular Nerve, Peking University Third Hospital, Beijing, China. alexlipingyang@bjmu.edu.cn. – Name: TitleSource Label: Source Group: Src Data: <searchLink fieldCode="JN" term="%22101528555%22">Nature communications</searchLink> [Nat Commun] 2024 May 06; Vol. 15 (1), pp. 3773. <i>Date of Electronic Publication: </i>2024 May 06. – Name: TypePub Label: Publication Type Group: TypPub Data: Journal Article; Research Support, Non-U.S. Gov't – Name: TitleSource Label: Journal Info Group: Src Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22Nature+Pub%2E+Group%22">Nature Pub. Group </searchLink><i>Country of Publication: </i>England <i>NLM ID: </i>101528555 <i>Publication Model: </i>Electronic <i>Cited Medium: </i>Internet <i>ISSN: </i>2041-1723 (Electronic) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2220411723%22">20411723 </searchLink><i>NLM ISO Abbreviation: </i>Nat Commun <i>Subsets: </i>MEDLINE |
| PLink | https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=mdl&AN=38710738 |
| RecordInfo | BibRecord: BibEntity: Identifiers: – Type: doi Value: 10.1038/s41467-024-48092-9 Languages: – Code: eng Text: English PhysicalDescription: Pagination: StartPage: 3773 Titles: – TitleFull: In vivo genome editing via CRISPR/Cas9-mediated homology-independent targeted integration for Bietti crystalline corneoretinal dystrophy treatment. Type: main BibRelationships: HasContributorRelationships: – PersonEntity: Name: NameFull: Meng X – PersonEntity: Name: NameFull: Jia R – PersonEntity: Name: NameFull: Zhao X – PersonEntity: Name: NameFull: Zhang F – PersonEntity: Name: NameFull: Chen S – PersonEntity: Name: NameFull: Yu S – PersonEntity: Name: NameFull: Liu X – PersonEntity: Name: NameFull: Dou H – PersonEntity: Name: NameFull: Feng X – PersonEntity: Name: NameFull: Zhang J – PersonEntity: Name: NameFull: Wang N – PersonEntity: Name: NameFull: Xu B – PersonEntity: Name: NameFull: Yang L IsPartOfRelationships: – BibEntity: Dates: – D: 06 M: 05 Text: 2024 May 06 Type: published Y: 2024 Identifiers: – Type: issn-electronic Value: 2041-1723 Numbering: – Type: volume Value: 15 – Type: issue Value: 1 Titles: – TitleFull: Nature communications Type: main |
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