Improvement in quality of life after asfotase alfa treatment in adults with pediatric-onset hypophosphatasia: data from 5 patient-reported outcome measures.

Saved in:
Bibliographic Details
Title: Improvement in quality of life after asfotase alfa treatment in adults with pediatric-onset hypophosphatasia: data from 5 patient-reported outcome measures.
Authors: Dahir KM; Endocrinology and Diabetes, Vanderbilt University Medical Center, Nashville, TN 37232, United States., Ing SW; Division of Endocrinology, Diabetes, and Metabolism, Wexner Medical Center, Ohio State University, Columbus, OH 43210, United States., Deal C; Department of Rheumatology, Center for Osteoporosis and Metabolic Bone Disease, Cleveland Clinic, Cleveland, OH 44195, United States., Messali A; Health Economics and Outcomes Research (AM) and Medical Affairs (CD), Alexion, AstraZeneca Rare Disease, Boston, MA 02210, United States., Bates T; Health Economics and Outcomes Research (AM) and Medical Affairs (CD), Alexion, AstraZeneca Rare Disease, Boston, MA 02210, United States., Rush ET; Division of Clinical Genetics, Children's Mercy Kansas City, Kansas City, MO 64108, United States.; Department of Pediatrics, University of Missouri - Kansas City School of Medicine, Kansas City, MO 64108, United States.
Source: JBMR plus [JBMR Plus] 2024 May 07; Vol. 8 (8), pp. ziae062. Date of Electronic Publication: 2024 May 07 (Print Publication: 2024).
Publication Type: Journal Article
Journal Info: Publisher: Oxford University Press Country of Publication: England NLM ID: 101707013 Publication Model: eCollection Cited Medium: Internet ISSN: 2473-4039 (Electronic) Linking ISSN: 24734039 NLM ISO Abbreviation: JBMR Plus Subsets: PubMed not MEDLINE
Database: MEDLINE Ultimate
Description
ISSN:2473-4039
DOI:10.1093/jbmrpl/ziae062