Improvement in quality of life after asfotase alfa treatment in adults with pediatric-onset hypophosphatasia: data from 5 patient-reported outcome measures.
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| Title: | Improvement in quality of life after asfotase alfa treatment in adults with pediatric-onset hypophosphatasia: data from 5 patient-reported outcome measures. |
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| Authors: | Dahir KM; Endocrinology and Diabetes, Vanderbilt University Medical Center, Nashville, TN 37232, United States., Ing SW; Division of Endocrinology, Diabetes, and Metabolism, Wexner Medical Center, Ohio State University, Columbus, OH 43210, United States., Deal C; Department of Rheumatology, Center for Osteoporosis and Metabolic Bone Disease, Cleveland Clinic, Cleveland, OH 44195, United States., Messali A; Health Economics and Outcomes Research (AM) and Medical Affairs (CD), Alexion, AstraZeneca Rare Disease, Boston, MA 02210, United States., Bates T; Health Economics and Outcomes Research (AM) and Medical Affairs (CD), Alexion, AstraZeneca Rare Disease, Boston, MA 02210, United States., Rush ET; Division of Clinical Genetics, Children's Mercy Kansas City, Kansas City, MO 64108, United States.; Department of Pediatrics, University of Missouri - Kansas City School of Medicine, Kansas City, MO 64108, United States. |
| Source: | JBMR plus [JBMR Plus] 2024 May 07; Vol. 8 (8), pp. ziae062. Date of Electronic Publication: 2024 May 07 (Print Publication: 2024). |
| Publication Type: | Journal Article |
| Journal Info: | Publisher: Oxford University Press Country of Publication: England NLM ID: 101707013 Publication Model: eCollection Cited Medium: Internet ISSN: 2473-4039 (Electronic) Linking ISSN: 24734039 NLM ISO Abbreviation: JBMR Plus Subsets: PubMed not MEDLINE |
| Database: | MEDLINE Ultimate |
| FullText | Links: – Type: pdflink Text: Availability: 0 |
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| Header | DbId: mdl DbLabel: MEDLINE Ultimate An: 39006866 AccessLevel: 2 PubType: Academic Journal PubTypeId: academicJournal PreciseRelevancyScore: 0 |
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| Items | – Name: Title Label: Title Group: Ti Data: Improvement in quality of life after asfotase alfa treatment in adults with pediatric-onset hypophosphatasia: data from 5 patient-reported outcome measures. – Name: Author Label: Authors Group: Au Data: <searchLink fieldCode="AU" term="%22Dahir+KM%22">Dahir KM</searchLink>; Endocrinology and Diabetes, Vanderbilt University Medical Center, Nashville, TN 37232, United States.<br /><searchLink fieldCode="AU" term="%22Ing+SW%22">Ing SW</searchLink>; Division of Endocrinology, Diabetes, and Metabolism, Wexner Medical Center, Ohio State University, Columbus, OH 43210, United States.<br /><searchLink fieldCode="AU" term="%22Deal+C%22">Deal C</searchLink>; Department of Rheumatology, Center for Osteoporosis and Metabolic Bone Disease, Cleveland Clinic, Cleveland, OH 44195, United States.<br /><searchLink fieldCode="AU" term="%22Messali+A%22">Messali A</searchLink>; Health Economics and Outcomes Research (AM) and Medical Affairs (CD), Alexion, AstraZeneca Rare Disease, Boston, MA 02210, United States.<br /><searchLink fieldCode="AU" term="%22Bates+T%22">Bates T</searchLink>; Health Economics and Outcomes Research (AM) and Medical Affairs (CD), Alexion, AstraZeneca Rare Disease, Boston, MA 02210, United States.<br /><searchLink fieldCode="AU" term="%22Rush+ET%22">Rush ET</searchLink>; Division of Clinical Genetics, Children's Mercy Kansas City, Kansas City, MO 64108, United States.; Department of Pediatrics, University of Missouri - Kansas City School of Medicine, Kansas City, MO 64108, United States. – Name: TitleSource Label: Source Group: Src Data: <searchLink fieldCode="JN" term="%22101707013%22">JBMR plus</searchLink> [JBMR Plus] 2024 May 07; Vol. 8 (8), pp. ziae062. <i>Date of Electronic Publication: </i>2024 May 07 (<i>Print Publication: </i>2024). – Name: TypePub Label: Publication Type Group: TypPub Data: Journal Article – Name: TitleSource Label: Journal Info Group: Src Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22Oxford+University+Press%22">Oxford University Press </searchLink><i>Country of Publication: </i>England <i>NLM ID: </i>101707013 <i>Publication Model: </i>eCollection <i>Cited Medium: </i>Internet <i>ISSN: </i>2473-4039 (Electronic) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2224734039%22">24734039 </searchLink><i>NLM ISO Abbreviation: </i>JBMR Plus <i>Subsets: </i>PubMed not MEDLINE |
| PLink | https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=mdl&AN=39006866 |
| RecordInfo | BibRecord: BibEntity: Identifiers: – Type: doi Value: 10.1093/jbmrpl/ziae062 Languages: – Code: eng Text: English PhysicalDescription: Pagination: StartPage: ziae062 Titles: – TitleFull: Improvement in quality of life after asfotase alfa treatment in adults with pediatric-onset hypophosphatasia: data from 5 patient-reported outcome measures. Type: main BibRelationships: HasContributorRelationships: – PersonEntity: Name: NameFull: Dahir KM – PersonEntity: Name: NameFull: Ing SW – PersonEntity: Name: NameFull: Deal C – PersonEntity: Name: NameFull: Messali A – PersonEntity: Name: NameFull: Bates T – PersonEntity: Name: NameFull: Rush ET IsPartOfRelationships: – BibEntity: Dates: – D: 07 M: 05 Text: 2024 May 07 Type: published Y: 2024 Identifiers: – Type: issn-electronic Value: 2473-4039 Numbering: – Type: volume Value: 8 – Type: issue Value: 8 Titles: – TitleFull: JBMR plus Type: main |
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