Improvement in quality of life after asfotase alfa treatment in adults with pediatric-onset hypophosphatasia: data from 5 patient-reported outcome measures.

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Title: Improvement in quality of life after asfotase alfa treatment in adults with pediatric-onset hypophosphatasia: data from 5 patient-reported outcome measures.
Authors: Dahir KM; Endocrinology and Diabetes, Vanderbilt University Medical Center, Nashville, TN 37232, United States., Ing SW; Division of Endocrinology, Diabetes, and Metabolism, Wexner Medical Center, Ohio State University, Columbus, OH 43210, United States., Deal C; Department of Rheumatology, Center for Osteoporosis and Metabolic Bone Disease, Cleveland Clinic, Cleveland, OH 44195, United States., Messali A; Health Economics and Outcomes Research (AM) and Medical Affairs (CD), Alexion, AstraZeneca Rare Disease, Boston, MA 02210, United States., Bates T; Health Economics and Outcomes Research (AM) and Medical Affairs (CD), Alexion, AstraZeneca Rare Disease, Boston, MA 02210, United States., Rush ET; Division of Clinical Genetics, Children's Mercy Kansas City, Kansas City, MO 64108, United States.; Department of Pediatrics, University of Missouri - Kansas City School of Medicine, Kansas City, MO 64108, United States.
Source: JBMR plus [JBMR Plus] 2024 May 07; Vol. 8 (8), pp. ziae062. Date of Electronic Publication: 2024 May 07 (Print Publication: 2024).
Publication Type: Journal Article
Journal Info: Publisher: Oxford University Press Country of Publication: England NLM ID: 101707013 Publication Model: eCollection Cited Medium: Internet ISSN: 2473-4039 (Electronic) Linking ISSN: 24734039 NLM ISO Abbreviation: JBMR Plus Subsets: PubMed not MEDLINE
Database: MEDLINE Ultimate
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  Data: Improvement in quality of life after asfotase alfa treatment in adults with pediatric-onset hypophosphatasia: data from 5 patient-reported outcome measures.
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  Data: <searchLink fieldCode="AU" term="%22Dahir+KM%22">Dahir KM</searchLink>; Endocrinology and Diabetes, Vanderbilt University Medical Center, Nashville, TN 37232, United States.<br /><searchLink fieldCode="AU" term="%22Ing+SW%22">Ing SW</searchLink>; Division of Endocrinology, Diabetes, and Metabolism, Wexner Medical Center, Ohio State University, Columbus, OH 43210, United States.<br /><searchLink fieldCode="AU" term="%22Deal+C%22">Deal C</searchLink>; Department of Rheumatology, Center for Osteoporosis and Metabolic Bone Disease, Cleveland Clinic, Cleveland, OH 44195, United States.<br /><searchLink fieldCode="AU" term="%22Messali+A%22">Messali A</searchLink>; Health Economics and Outcomes Research (AM) and Medical Affairs (CD), Alexion, AstraZeneca Rare Disease, Boston, MA 02210, United States.<br /><searchLink fieldCode="AU" term="%22Bates+T%22">Bates T</searchLink>; Health Economics and Outcomes Research (AM) and Medical Affairs (CD), Alexion, AstraZeneca Rare Disease, Boston, MA 02210, United States.<br /><searchLink fieldCode="AU" term="%22Rush+ET%22">Rush ET</searchLink>; Division of Clinical Genetics, Children's Mercy Kansas City, Kansas City, MO 64108, United States.; Department of Pediatrics, University of Missouri - Kansas City School of Medicine, Kansas City, MO 64108, United States.
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  Data: <searchLink fieldCode="JN" term="%22101707013%22">JBMR plus</searchLink> [JBMR Plus] 2024 May 07; Vol. 8 (8), pp. ziae062. <i>Date of Electronic Publication: </i>2024 May 07 (<i>Print Publication: </i>2024).
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        Value: 10.1093/jbmrpl/ziae062
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      – TitleFull: Improvement in quality of life after asfotase alfa treatment in adults with pediatric-onset hypophosphatasia: data from 5 patient-reported outcome measures.
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