Activated factor X delivered by adeno-associated virus significantly inhibited bleeding and alleviated hemophilic synovitis in hemophilic mice.

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Bibliographic Details
Title: Activated factor X delivered by adeno-associated virus significantly inhibited bleeding and alleviated hemophilic synovitis in hemophilic mice.
Authors: Zhang F; School of Biotechnology, East China University of Science and Technology, Shanghai, China., Zhou X; School of Pharmacy, East China University of Science and Technology, Shanghai, China., Hua B; Department of Hematology, Beijing Shijitan Hospital, Capital Medical University, Beijing, China., He X; School of Pharmacy, East China University of Science and Technology, Shanghai, China., Li Z; School of Pharmacy, East China University of Science and Technology, Shanghai, China., Xiao X; School of Biotechnology, East China University of Science and Technology, Shanghai, China.; School of Pharmacy, East China University of Science and Technology, Shanghai, China., Wu X; School of Pharmacy, East China University of Science and Technology, Shanghai, China. wuxia@ecust.edu.cn.
Source: Gene therapy [Gene Ther] 2024 Nov; Vol. 31 (11-12), pp. 544-552. Date of Electronic Publication: 2024 Sep 10.
Publication Type: Journal Article; Research Support, Non-U.S. Gov't
Journal Info: Publisher: Nature Publishing Group Country of Publication: England NLM ID: 9421525 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1476-5462 (Electronic) Linking ISSN: 09697128 NLM ISO Abbreviation: Gene Ther Subsets: MEDLINE
Database: MEDLINE Ultimate
Description
ISSN:1476-5462
DOI:10.1038/s41434-024-00479-5