Durable suppression of seizures in a preclinical model of KCNT1 genetic epilepsy with divalent small interfering RNA.
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| Title: | Durable suppression of seizures in a preclinical model of KCNT1 genetic epilepsy with divalent small interfering RNA. |
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| Authors: | Andreone BJ; Atalanta Therapeutics, Boston, Massachusetts, USA., Lin J; Atalanta Therapeutics, Boston, Massachusetts, USA., Tocci J; Atalanta Therapeutics, Boston, Massachusetts, USA., Rook M; Atalanta Therapeutics, Boston, Massachusetts, USA., Omer A; Atalanta Therapeutics, Boston, Massachusetts, USA., Carito LM; Atalanta Therapeutics, Boston, Massachusetts, USA., Yang C; Atalanta Therapeutics, Boston, Massachusetts, USA., Zhoba H; Atalanta Therapeutics, Boston, Massachusetts, USA., DeJesus C; Atalanta Therapeutics, Boston, Massachusetts, USA., Traore M; Atalanta Therapeutics, Boston, Massachusetts, USA., Haruehanroengra P; Atalanta Therapeutics, Boston, Massachusetts, USA., Prinzen A; Atalanta Therapeutics, Boston, Massachusetts, USA., Miglis G; Atalanta Therapeutics, Boston, Massachusetts, USA., Deninger M; Atalanta Therapeutics, Boston, Massachusetts, USA., Li M; Atalanta Therapeutics, Boston, Massachusetts, USA., Lynch T; Atalanta Therapeutics, Boston, Massachusetts, USA., Howat B; Atalanta Therapeutics, Boston, Massachusetts, USA., Rogers KA; Atalanta Therapeutics, Boston, Massachusetts, USA., Gallant-Behm CL; Atalanta Therapeutics, Boston, Massachusetts, USA., Kinberger GA; Atalanta Therapeutics, Boston, Massachusetts, USA., Yudowski G; Atalanta Therapeutics, Boston, Massachusetts, USA., Chen Q; Atalanta Therapeutics, Boston, Massachusetts, USA., Jackson AL; Atalanta Therapeutics, Boston, Massachusetts, USA., McDonough SI; Atalanta Therapeutics, Boston, Massachusetts, USA. |
| Source: | Epilepsia [Epilepsia] 2025 May; Vol. 66 (5), pp. 1677-1690. Date of Electronic Publication: 2025 Jan 27. |
| Publication Type: | Journal Article |
| Journal Info: | Publisher: Blackwell Science Country of Publication: United States NLM ID: 2983306R Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1528-1167 (Electronic) Linking ISSN: 00139580 NLM ISO Abbreviation: Epilepsia Subsets: MEDLINE |
| Database: | MEDLINE Ultimate |
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| ISSN: | 1528-1167 |
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| DOI: | 10.1111/epi.18278 |