Durable suppression of seizures in a preclinical model of KCNT1 genetic epilepsy with divalent small interfering RNA.

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Title: Durable suppression of seizures in a preclinical model of KCNT1 genetic epilepsy with divalent small interfering RNA.
Authors: Andreone BJ; Atalanta Therapeutics, Boston, Massachusetts, USA., Lin J; Atalanta Therapeutics, Boston, Massachusetts, USA., Tocci J; Atalanta Therapeutics, Boston, Massachusetts, USA., Rook M; Atalanta Therapeutics, Boston, Massachusetts, USA., Omer A; Atalanta Therapeutics, Boston, Massachusetts, USA., Carito LM; Atalanta Therapeutics, Boston, Massachusetts, USA., Yang C; Atalanta Therapeutics, Boston, Massachusetts, USA., Zhoba H; Atalanta Therapeutics, Boston, Massachusetts, USA., DeJesus C; Atalanta Therapeutics, Boston, Massachusetts, USA., Traore M; Atalanta Therapeutics, Boston, Massachusetts, USA., Haruehanroengra P; Atalanta Therapeutics, Boston, Massachusetts, USA., Prinzen A; Atalanta Therapeutics, Boston, Massachusetts, USA., Miglis G; Atalanta Therapeutics, Boston, Massachusetts, USA., Deninger M; Atalanta Therapeutics, Boston, Massachusetts, USA., Li M; Atalanta Therapeutics, Boston, Massachusetts, USA., Lynch T; Atalanta Therapeutics, Boston, Massachusetts, USA., Howat B; Atalanta Therapeutics, Boston, Massachusetts, USA., Rogers KA; Atalanta Therapeutics, Boston, Massachusetts, USA., Gallant-Behm CL; Atalanta Therapeutics, Boston, Massachusetts, USA., Kinberger GA; Atalanta Therapeutics, Boston, Massachusetts, USA., Yudowski G; Atalanta Therapeutics, Boston, Massachusetts, USA., Chen Q; Atalanta Therapeutics, Boston, Massachusetts, USA., Jackson AL; Atalanta Therapeutics, Boston, Massachusetts, USA., McDonough SI; Atalanta Therapeutics, Boston, Massachusetts, USA.
Source: Epilepsia [Epilepsia] 2025 May; Vol. 66 (5), pp. 1677-1690. Date of Electronic Publication: 2025 Jan 27.
Publication Type: Journal Article
Journal Info: Publisher: Blackwell Science Country of Publication: United States NLM ID: 2983306R Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1528-1167 (Electronic) Linking ISSN: 00139580 NLM ISO Abbreviation: Epilepsia Subsets: MEDLINE
Database: MEDLINE Ultimate
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  Data: Durable suppression of seizures in a preclinical model of KCNT1 genetic epilepsy with divalent small interfering RNA.
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  Data: <searchLink fieldCode="JN" term="%222983306R%22">Epilepsia</searchLink> [Epilepsia] 2025 May; Vol. 66 (5), pp. 1677-1690. <i>Date of Electronic Publication: </i>2025 Jan 27.
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  Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22Blackwell+Science%22">Blackwell Science </searchLink><i>Country of Publication: </i>United States <i>NLM ID: </i>2983306R <i>Publication Model: </i>Print-Electronic <i>Cited Medium: </i>Internet <i>ISSN: </i>1528-1167 (Electronic) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2200139580%22">00139580 </searchLink><i>NLM ISO Abbreviation: </i>Epilepsia <i>Subsets: </i>MEDLINE
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        Value: 10.1111/epi.18278
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              Text: 2025 May
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