The PROPHECI trial: a phase II, double-blind, placebo-controlled, randomized clinical trial for the treatment of pseudoxanthoma elasticum with oral pyrophosphate.

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Title: The PROPHECI trial: a phase II, double-blind, placebo-controlled, randomized clinical trial for the treatment of pseudoxanthoma elasticum with oral pyrophosphate.
Authors: Clotaire L; Université Côte d'Azur, CNRS, LP2M, Nice, France.; Research and Development Department, Laboratoires ProNutri, Carros, France., Rubera I; Université Côte d'Azur, CNRS, LP2M, Nice, France., Duranton C; Université Côte d'Azur, CNRS, LP2M, Nice, France., Gal J; Statistics Department, Centre Antoine Lacassagne, Nice, France., Chamorey E; Statistics Department, Centre Antoine Lacassagne, Nice, France., Humeau H; Ophthalmology Department, Centre Hospitalo-Universitaire d'Angers, Angers, France., Yamani S; Drug Safety Department, Université Côte d'Azur, Centre Hospitalier Universitaire de Nice, Nice, France., Chiaverini C; Dermatology Department, Université Côte d'Azur, Centre Hospitalier Universitaire de Nice, Nice, France., Willoteaux S; Radiology Department, Centre Hospitalo-Universitaire d'Angers, Angers, France., Padovani B; Radiology Department, Université Côte d'Azur, Centre Hospitalier Universitaire de Nice, Nice, France., Mourozeau L; Ophthalmology Department, Centre Hospitalo-Universitaire d'Angers, Angers, France., Mainguy A; Ophthalmology Department, Centre Hospitalo-Universitaire d'Angers, Angers, France., Baillif S; Ophthalmology Department, Université Côte d'Azur, Centre Hospitalier Universitaire de Nice, Nice, France., Martin L; Centre Hospitalo-Universitaire d'Angers, PXE National Reference Center, Angers, France.; Dermatology Department, Centre Hospitalo-Universitaire d'Angers, Angers, France., Leftheriotis G; Université Côte d'Azur, CNRS, LP2M, Nice, France. leftheriotis.g@chu-nice.fr.; National Center for Rare Arterial Diseases, Université Côte d'Azur, Centre Hospitalier Universitaire de Nice, Nice, France. leftheriotis.g@chu-nice.fr.
Source: Trials [Trials] 2025 Jan 29; Vol. 26 (1), pp. 30. Date of Electronic Publication: 2025 Jan 29.
Publication Type: Clinical Trial Protocol; Journal Article
Journal Info: Publisher: BioMed Central Country of Publication: England NLM ID: 101263253 Publication Model: Electronic Cited Medium: Internet ISSN: 1745-6215 (Electronic) Linking ISSN: 17456215 NLM ISO Abbreviation: Trials Subsets: MEDLINE
Database: MEDLINE Ultimate
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ISSN:1745-6215
DOI:10.1186/s13063-024-08666-w