The PROPHECI trial: a phase II, double-blind, placebo-controlled, randomized clinical trial for the treatment of pseudoxanthoma elasticum with oral pyrophosphate.
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| Title: | The PROPHECI trial: a phase II, double-blind, placebo-controlled, randomized clinical trial for the treatment of pseudoxanthoma elasticum with oral pyrophosphate. |
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| Authors: | Clotaire L; Université Côte d'Azur, CNRS, LP2M, Nice, France.; Research and Development Department, Laboratoires ProNutri, Carros, France., Rubera I; Université Côte d'Azur, CNRS, LP2M, Nice, France., Duranton C; Université Côte d'Azur, CNRS, LP2M, Nice, France., Gal J; Statistics Department, Centre Antoine Lacassagne, Nice, France., Chamorey E; Statistics Department, Centre Antoine Lacassagne, Nice, France., Humeau H; Ophthalmology Department, Centre Hospitalo-Universitaire d'Angers, Angers, France., Yamani S; Drug Safety Department, Université Côte d'Azur, Centre Hospitalier Universitaire de Nice, Nice, France., Chiaverini C; Dermatology Department, Université Côte d'Azur, Centre Hospitalier Universitaire de Nice, Nice, France., Willoteaux S; Radiology Department, Centre Hospitalo-Universitaire d'Angers, Angers, France., Padovani B; Radiology Department, Université Côte d'Azur, Centre Hospitalier Universitaire de Nice, Nice, France., Mourozeau L; Ophthalmology Department, Centre Hospitalo-Universitaire d'Angers, Angers, France., Mainguy A; Ophthalmology Department, Centre Hospitalo-Universitaire d'Angers, Angers, France., Baillif S; Ophthalmology Department, Université Côte d'Azur, Centre Hospitalier Universitaire de Nice, Nice, France., Martin L; Centre Hospitalo-Universitaire d'Angers, PXE National Reference Center, Angers, France.; Dermatology Department, Centre Hospitalo-Universitaire d'Angers, Angers, France., Leftheriotis G; Université Côte d'Azur, CNRS, LP2M, Nice, France. leftheriotis.g@chu-nice.fr.; National Center for Rare Arterial Diseases, Université Côte d'Azur, Centre Hospitalier Universitaire de Nice, Nice, France. leftheriotis.g@chu-nice.fr. |
| Source: | Trials [Trials] 2025 Jan 29; Vol. 26 (1), pp. 30. Date of Electronic Publication: 2025 Jan 29. |
| Publication Type: | Clinical Trial Protocol; Journal Article |
| Journal Info: | Publisher: BioMed Central Country of Publication: England NLM ID: 101263253 Publication Model: Electronic Cited Medium: Internet ISSN: 1745-6215 (Electronic) Linking ISSN: 17456215 NLM ISO Abbreviation: Trials Subsets: MEDLINE |
| Database: | MEDLINE Ultimate |
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| FullText | Links: – Type: pdflink Text: Availability: 1 |
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| Header | DbId: mdl DbLabel: MEDLINE Ultimate An: 39881395 AccessLevel: 2 PubType: Academic Journal PubTypeId: academicJournal PreciseRelevancyScore: 0 |
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| Items | – Name: Title Label: Title Group: Ti Data: The PROPHECI trial: a phase II, double-blind, placebo-controlled, randomized clinical trial for the treatment of pseudoxanthoma elasticum with oral pyrophosphate. – Name: Author Label: Authors Group: Au Data: <searchLink fieldCode="AU" term="%22Clotaire+L%22">Clotaire L</searchLink>; Université Côte d'Azur, CNRS, LP2M, Nice, France.; Research and Development Department, Laboratoires ProNutri, Carros, France.<br /><searchLink fieldCode="AU" term="%22Rubera+I%22">Rubera I</searchLink>; Université Côte d'Azur, CNRS, LP2M, Nice, France.<br /><searchLink fieldCode="AU" term="%22Duranton+C%22">Duranton C</searchLink>; Université Côte d'Azur, CNRS, LP2M, Nice, France.<br /><searchLink fieldCode="AU" term="%22Gal+J%22">Gal J</searchLink>; Statistics Department, Centre Antoine Lacassagne, Nice, France.<br /><searchLink fieldCode="AU" term="%22Chamorey+E%22">Chamorey E</searchLink>; Statistics Department, Centre Antoine Lacassagne, Nice, France.<br /><searchLink fieldCode="AU" term="%22Humeau+H%22">Humeau H</searchLink>; Ophthalmology Department, Centre Hospitalo-Universitaire d'Angers, Angers, France.<br /><searchLink fieldCode="AU" term="%22Yamani+S%22">Yamani S</searchLink>; Drug Safety Department, Université Côte d'Azur, Centre Hospitalier Universitaire de Nice, Nice, France.<br /><searchLink fieldCode="AU" term="%22Chiaverini+C%22">Chiaverini C</searchLink>; Dermatology Department, Université Côte d'Azur, Centre Hospitalier Universitaire de Nice, Nice, France.<br /><searchLink fieldCode="AU" term="%22Willoteaux+S%22">Willoteaux S</searchLink>; Radiology Department, Centre Hospitalo-Universitaire d'Angers, Angers, France.<br /><searchLink fieldCode="AU" term="%22Padovani+B%22">Padovani B</searchLink>; Radiology Department, Université Côte d'Azur, Centre Hospitalier Universitaire de Nice, Nice, France.<br /><searchLink fieldCode="AU" term="%22Mourozeau+L%22">Mourozeau L</searchLink>; Ophthalmology Department, Centre Hospitalo-Universitaire d'Angers, Angers, France.<br /><searchLink fieldCode="AU" term="%22Mainguy+A%22">Mainguy A</searchLink>; Ophthalmology Department, Centre Hospitalo-Universitaire d'Angers, Angers, France.<br /><searchLink fieldCode="AU" term="%22Baillif+S%22">Baillif S</searchLink>; Ophthalmology Department, Université Côte d'Azur, Centre Hospitalier Universitaire de Nice, Nice, France.<br /><searchLink fieldCode="AU" term="%22Martin+L%22">Martin L</searchLink>; Centre Hospitalo-Universitaire d'Angers, PXE National Reference Center, Angers, France.; Dermatology Department, Centre Hospitalo-Universitaire d'Angers, Angers, France.<br /><searchLink fieldCode="AU" term="%22Leftheriotis+G%22">Leftheriotis G</searchLink>; Université Côte d'Azur, CNRS, LP2M, Nice, France. leftheriotis.g@chu-nice.fr.; National Center for Rare Arterial Diseases, Université Côte d'Azur, Centre Hospitalier Universitaire de Nice, Nice, France. leftheriotis.g@chu-nice.fr. – Name: TitleSource Label: Source Group: Src Data: <searchLink fieldCode="JN" term="%22101263253%22">Trials</searchLink> [Trials] 2025 Jan 29; Vol. 26 (1), pp. 30. <i>Date of Electronic Publication: </i>2025 Jan 29. – Name: TypePub Label: Publication Type Group: TypPub Data: Clinical Trial Protocol; Journal Article – Name: TitleSource Label: Journal Info Group: Src Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22BioMed+Central%22">BioMed Central </searchLink><i>Country of Publication: </i>England <i>NLM ID: </i>101263253 <i>Publication Model: </i>Electronic <i>Cited Medium: </i>Internet <i>ISSN: </i>1745-6215 (Electronic) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2217456215%22">17456215 </searchLink><i>NLM ISO Abbreviation: </i>Trials <i>Subsets: </i>MEDLINE |
| PLink | https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=mdl&AN=39881395 |
| RecordInfo | BibRecord: BibEntity: Identifiers: – Type: doi Value: 10.1186/s13063-024-08666-w Languages: – Code: eng Text: English PhysicalDescription: Pagination: StartPage: 30 Titles: – TitleFull: The PROPHECI trial: a phase II, double-blind, placebo-controlled, randomized clinical trial for the treatment of pseudoxanthoma elasticum with oral pyrophosphate. Type: main BibRelationships: HasContributorRelationships: – PersonEntity: Name: NameFull: Clotaire L – PersonEntity: Name: NameFull: Rubera I – PersonEntity: Name: NameFull: Duranton C – PersonEntity: Name: NameFull: Gal J – PersonEntity: Name: NameFull: Chamorey E – PersonEntity: Name: NameFull: Humeau H – PersonEntity: Name: NameFull: Yamani S – PersonEntity: Name: NameFull: Chiaverini C – PersonEntity: Name: NameFull: Willoteaux S – PersonEntity: Name: NameFull: Padovani B – PersonEntity: Name: NameFull: Mourozeau L – PersonEntity: Name: NameFull: Mainguy A – PersonEntity: Name: NameFull: Baillif S – PersonEntity: Name: NameFull: Martin L – PersonEntity: Name: NameFull: Leftheriotis G IsPartOfRelationships: – BibEntity: Dates: – D: 29 M: 01 Text: 2025 Jan 29 Type: published Y: 2025 Identifiers: – Type: issn-electronic Value: 1745-6215 Numbering: – Type: volume Value: 26 – Type: issue Value: 1 Titles: – TitleFull: Trials Type: main |
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