High-throughput in vitro drug screening and in vivo studies identify fenretinide as a brain-penetrant DMG therapeutic.

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Title: High-throughput in vitro drug screening and in vivo studies identify fenretinide as a brain-penetrant DMG therapeutic.
Authors: Upton DH; School of Clinical Medicine, University of New South Wales, Sydney, NSW, Australia.; Children's Cancer Institute, Lowy Cancer Research Centre, University of New South Wales, Sydney, NSW, Australia., Liu J; Children's Cancer Institute, Lowy Cancer Research Centre, University of New South Wales, Sydney, NSW, Australia., George SM; Children's Cancer Institute, Lowy Cancer Research Centre, University of New South Wales, Sydney, NSW, Australia., Valvi S; Children's Cancer Institute, Lowy Cancer Research Centre, University of New South Wales, Sydney, NSW, Australia., Ung C; Children's Cancer Institute, Lowy Cancer Research Centre, University of New South Wales, Sydney, NSW, Australia., Rayner BS; School of Clinical Medicine, University of New South Wales, Sydney, NSW, Australia.; Children's Cancer Institute, Lowy Cancer Research Centre, University of New South Wales, Sydney, NSW, Australia., Gopalakrishnan A; Children's Cancer Institute, Lowy Cancer Research Centre, University of New South Wales, Sydney, NSW, Australia., Pandher R; School of Clinical Medicine, University of New South Wales, Sydney, NSW, Australia.; Children's Cancer Institute, Lowy Cancer Research Centre, University of New South Wales, Sydney, NSW, Australia., Khan A; School of Clinical Medicine, University of New South Wales, Sydney, NSW, Australia.; Children's Cancer Institute, Lowy Cancer Research Centre, University of New South Wales, Sydney, NSW, Australia., Venkat P; Children's Cancer Institute, Lowy Cancer Research Centre, University of New South Wales, Sydney, NSW, Australia., Mayoh C; School of Clinical Medicine, University of New South Wales, Sydney, NSW, Australia.; Children's Cancer Institute, Lowy Cancer Research Centre, University of New South Wales, Sydney, NSW, Australia., Holliday H; School of Clinical Medicine, University of New South Wales, Sydney, NSW, Australia.; Children's Cancer Institute, Lowy Cancer Research Centre, University of New South Wales, Sydney, NSW, Australia., Yeung N; Children's Cancer Institute, Lowy Cancer Research Centre, University of New South Wales, Sydney, NSW, Australia., Nguyen H; Children's Cancer Institute, Lowy Cancer Research Centre, University of New South Wales, Sydney, NSW, Australia., Franshaw L; Children's Cancer Institute, Lowy Cancer Research Centre, University of New South Wales, Sydney, NSW, Australia., Ehteda A; Children's Cancer Institute, Lowy Cancer Research Centre, University of New South Wales, Sydney, NSW, Australia., Shen H; Children's Cancer Institute, Lowy Cancer Research Centre, University of New South Wales, Sydney, NSW, Australia., Farruggia G; Alma Mater Studiorum University of Bologna, Department of Pharmacy and Biotechnology, Bologna, Italy., Orienti I; Alma Mater Studiorum University of Bologna, Department of Pharmacy and Biotechnology, Bologna, Italy., Reynolds CP; Cancer Center, School of Medicine, Texas Tech University Health Sciences Center, Lubbock, TX, USA., Tsoli M; School of Clinical Medicine, University of New South Wales, Sydney, NSW, Australia.; Children's Cancer Institute, Lowy Cancer Research Centre, University of New South Wales, Sydney, NSW, Australia., Ziegler DS; Kid's Cancer Centre, Sydney Children's Hospital, Randwick, NSW, Australia.; School of Clinical Medicine, University of New South Wales, Sydney, NSW, Australia.; Children's Cancer Institute, Lowy Cancer Research Centre, University of New South Wales, Sydney, NSW, Australia.
Source: Neuro-oncology [Neuro Oncol] 2025 Sep 08; Vol. 27 (7), pp. 1813-1828.
Publication Type: Journal Article
Journal Info: Publisher: Oxford University Press Country of Publication: England NLM ID: 100887420 Publication Model: Print Cited Medium: Internet ISSN: 1523-5866 (Electronic) Linking ISSN: 15228517 NLM ISO Abbreviation: Neuro Oncol Subsets: MEDLINE
Database: MEDLINE Ultimate
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ISSN:1523-5866
DOI:10.1093/neuonc/noaf035