The road toward AAV-mediated gene therapy of Duchenne muscular dystrophy.

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Bibliographic Details
Title: The road toward AAV-mediated gene therapy of Duchenne muscular dystrophy.
Authors: Bengtsson NE; Department of Neurology, University of Washington School of Medicine, Seattle, WA 98109, USA; Senator Paul D. Wellstone Muscular Dystrophy Specialized Research Center, University of Washington School of Medicine, Seattle, WA 98109, USA. Electronic address: niclasb@uw.edu., Tasfaout H; Department of Neurology, University of Washington School of Medicine, Seattle, WA 98109, USA; Senator Paul D. Wellstone Muscular Dystrophy Specialized Research Center, University of Washington School of Medicine, Seattle, WA 98109, USA. Electronic address: tasfaout@uw.edu., Chamberlain JS; Department of Neurology, University of Washington School of Medicine, Seattle, WA 98109, USA; Senator Paul D. Wellstone Muscular Dystrophy Specialized Research Center, University of Washington School of Medicine, Seattle, WA 98109, USA; Department of Medicine, University of Washington School of Medicine, Seattle, WA 98109, USA; Department of Biochemistry, University of Washington School of Medicine, Seattle, WA 98109, USA. Electronic address: jsc5@uw.edu.
Source: Molecular therapy : the journal of the American Society of Gene Therapy [Mol Ther] 2025 May 07; Vol. 33 (5), pp. 2035-2051. Date of Electronic Publication: 2025 Apr 02.
Publication Type: Journal Article; Review
Journal Info: Publisher: Cell Press Country of Publication: United States NLM ID: 100890581 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1525-0024 (Electronic) Linking ISSN: 15250016 NLM ISO Abbreviation: Mol Ther Subsets: MEDLINE
Database: MEDLINE Ultimate
Description
ISSN:1525-0024
DOI:10.1016/j.ymthe.2025.03.065