| Authors: |
Byrne BJ; Powell Gene Therapy Center, University of Florida College of Medicine, Gainesville, FL, USA; Department of Pediatrics, University of Florida College of Medicine, Gainesville, FL, USA. Electronic address: barry.byrne@ufl.edu., Flanigan KM; Center for Gene Therapy, Nationwide Children's Hospital, Columbus, OH, USA; Department of Pediatrics and Neurology, The Ohio State University, Columbus, OH, USA., Matesanz SE; Clinical In Vivo Gene Therapy, Children's Hospital of Philadelphia, Philadelphia, PA, USA; Department of Neurology, University of Pennsylvania School of Medicine, Philadelphia, Philadelphia, PA, USA., Finkel RS; Center for Experimental Neurotherapeutics, St. Jude Children's Research Hospital, Memphis, TN, USA., Waldrop MA; Center for Gene Therapy, Nationwide Children's Hospital, Columbus, OH, USA; Department of Pediatrics and Neurology, The Ohio State University, Columbus, OH, USA., D'Ambrosio ES; Department of Neurology, University of Massachusetts Chan School of Medicine, Worcester, MA, USA., Johnson NE; Department of Neurology and Center for Inherited Muscle Research, Virginia Commonwealth University, Richmond, VA, USA., Smith BK; Department of Physical Therapy, College of Public Health and Health Professions, University of Florida Gainesville, FL, USA., Bönnemann C; Neuromuscular and Neurogenetic Disorders of Childhood, NINDS/NIH, Bethesda, MD, USA., Carrig S; Clinical In Vivo Gene Therapy, Children's Hospital of Philadelphia, Philadelphia, PA, USA., Rossano JW; Department of Pediatrics, University of Pennsylvania School of Medicine, Philadelphia, PA, USA; Division of Cardiology, Children's Hospital of Philadelphia, Philadelphia PA, USA., Greenberg B; Cardiology Department, University of California, California, San Diego, La Jolla, CA, USA., Lalaguna L; Centro Nacional de Investigaciones Cardiovasculares Carlos III (CNIC), Madrid, Spain., Lara-Pezzi E; Centro Nacional de Investigaciones Cardiovasculares Carlos III (CNIC), Madrid, Spain; Centro de Investigación Biomédica en Red Cardiovascular (CIBERCV), Madrid, Spain., Subramony S; Department of Neurology, University of Florida College of Medicinem, Gainesville, FL, USA., Corti M; Powell Gene Therapy Center, University of Florida College of Medicine, Gainesville, FL, USA; Department of Pediatrics, University of Florida College of Medicine, Gainesville, FL, USA., Mercado-Rodriguez C; Powell Gene Therapy Center, University of Florida College of Medicine, Gainesville, FL, USA., Leon-Astudillo C; Department of Pediatrics, University of Florida College of Medicine, Gainesville, FL, USA., Ahrens-Nicklas R; Clinical In Vivo Gene Therapy, Children's Hospital of Philadelphia, Philadelphia, PA, USA; Department of Pediatrics, University of Pennsylvania School of Medicine, Philadelphia, PA, USA., Bharucha-Goebel D; Neuromuscular and Neurogenetic Disorders of Childhood, NINDS/NIH, Bethesda, MD, USA; Division of Neurology, Children's National Hospital, Washington, DC, USA., Gao G; Department of Genetic and Cellular Medicine, Horae Gene Therapy Center, University of Massachusetts Chan School of Medicine, Worcester, MA, USA., Gessler DJ; Department of Genetic and Cellular Medicine, Horae Gene Therapy Center, University of Massachusetts Chan School of Medicine, Worcester, MA, USA., Hwu WL; Department of Medical Genetics and Pediatrics, National Taiwan University Hospital, and College of Medicine, National Taiwan University, Taipei, Taiwan; Center for Precision Medicine, China Medical University Hospital, Taichung, Taiwan., Chien YH; Department of Medical Genetics and Pediatrics, National Taiwan University Hospital, and College of Medicine, National Taiwan University, Taipei, Taiwan., Lee NC; Department of Medical Genetics and Pediatrics, National Taiwan University Hospital, and College of Medicine, National Taiwan University, Taipei, Taiwan., Boye SL; Powell Gene Therapy Center, University of Florida College of Medicine, Gainesville, FL, USA; Department of Pediatrics, University of Florida College of Medicine, Gainesville, FL, USA., Boye SE; Powell Gene Therapy Center, University of Florida College of Medicine, Gainesville, FL, USA; Division of Cellular and Molecular Therapy, Department of Pediatrics, University of Florida College of Medicine, Gainesville, FL, USA., George LA; Clinical In Vivo Gene Therapy, Children's Hospital of Philadelphia, Philadelphia, PA, USA; Department of Pediatrics, University of Pennsylvania School of Medicine, Philadelphia, PA, USA. Electronic address: georgel@chop.edu. |
