Treatment of a metabolic liver disease in mice with a transient prime editing approach.

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Title: Treatment of a metabolic liver disease in mice with a transient prime editing approach.
Authors: Rothgangl T; Institute of Pharmacology and Toxicology, University of Zurich, Zurich, Switzerland., Tálas A; Institute of Pharmacology and Toxicology, University of Zurich, Zurich, Switzerland., Ioannidi EI; Institute of Pharmacology and Toxicology, University of Zurich, Zurich, Switzerland., Weber Y; Institute of Pharmacology and Toxicology, University of Zurich, Zurich, Switzerland., Böck D; Institute of Pharmacology and Toxicology, University of Zurich, Zurich, Switzerland., Matsushita M; Institute of Molecular Health Sciences, ETH Zurich, Zurich, Switzerland., Villiger EA; Institute of Pharmacology and Toxicology, University of Zurich, Zurich, Switzerland., Schmidheini L; Institute of Pharmacology and Toxicology, University of Zurich, Zurich, Switzerland.; Institute of Molecular Health Sciences, ETH Zurich, Zurich, Switzerland., Moon WJ; Acuitas Therapeutics Inc., Vancouver, British Columbia, Canada., Lin PJC; Acuitas Therapeutics Inc., Vancouver, British Columbia, Canada., Fan SHY; Acuitas Therapeutics Inc., Vancouver, British Columbia, Canada., Marquart KF; Institute of Pharmacology and Toxicology, University of Zurich, Zurich, Switzerland.; Institute of Molecular Health Sciences, ETH Zurich, Zurich, Switzerland., Schwerdel C; Institute of Pharmacology and Toxicology, University of Zurich, Zurich, Switzerland., Rimann N; Division of Metabolism and Children's Research Center, University Children's Hospital Zurich, Zurich, Switzerland., Faccin E; Division of Metabolism and Children's Research Center, University Children's Hospital Zurich, Zurich, Switzerland., Villiger L; Institute of Pharmacology and Toxicology, University of Zurich, Zurich, Switzerland., Muramatsu H; Department of Microbiology, Perelman School of Medicine, University of Pennsylvania, Philadelphia, PA, USA., Vadovics M; Department of Microbiology, Perelman School of Medicine, University of Pennsylvania, Philadelphia, PA, USA., Cremonesi A; Division of Clinical Chemistry and Biochemistry, University Children's Hospital Zurich, University of Zurich, Zurich, Switzerland., Kulcsár PI; Institute of Pharmacology and Toxicology, University of Zurich, Zurich, Switzerland., Thöny B; Division of Metabolism and Children's Research Center, University Children's Hospital Zurich, Zurich, Switzerland., Kopf M; Institute of Molecular Health Sciences, ETH Zurich, Zurich, Switzerland., Häberle J; Division of Metabolism and Children's Research Center, University Children's Hospital Zurich, Zurich, Switzerland., Pardi N; Department of Microbiology, Perelman School of Medicine, University of Pennsylvania, Philadelphia, PA, USA., Tam YK; Acuitas Therapeutics Inc., Vancouver, British Columbia, Canada., Schwank G; Institute of Pharmacology and Toxicology, University of Zurich, Zurich, Switzerland. gerald.schwank@uzh.ch.
Source: Nature biomedical engineering [Nat Biomed Eng] 2025 Oct; Vol. 9 (10), pp. 1705-1718. Date of Electronic Publication: 2025 May 20.
Publication Type: Journal Article
Journal Info: Publisher: Springer Nature Country of Publication: England NLM ID: 101696896 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 2157-846X (Electronic) Linking ISSN: 2157846X NLM ISO Abbreviation: Nat Biomed Eng Subsets: MEDLINE
Database: MEDLINE Ultimate
Description
ISSN:2157-846X
DOI:10.1038/s41551-025-01399-4