Prenatal Elexacaftor/Tezacaftor/Ivacaftor Treatment Prevents Meconium Ileus, but Not Exocrine Pancreatic Insufficiency and Lung Disease in Infants With Cystic Fibrosis.

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Title: Prenatal Elexacaftor/Tezacaftor/Ivacaftor Treatment Prevents Meconium Ileus, but Not Exocrine Pancreatic Insufficiency and Lung Disease in Infants With Cystic Fibrosis.
Authors: Aleksander PE; Department of Pediatric Respiratory Medicine, Immunology and Critical Care Medicine, Charité - Universitätsmedizin Berlin, Berlin, Germany.; German Center for Child and Adolescent Health (DZKJ), Partner Site Berlin, Berlin, Germany.; German Center for Lung Research (DZL), Associated Partner Site Berlin, Berlin, Germany., Thee S; Department of Pediatric Respiratory Medicine, Immunology and Critical Care Medicine, Charité - Universitätsmedizin Berlin, Berlin, Germany.; German Center for Child and Adolescent Health (DZKJ), Partner Site Berlin, Berlin, Germany.; German Center for Lung Research (DZL), Associated Partner Site Berlin, Berlin, Germany.; Berlin Institute of Health (BIH) at Charité, Berlin, Germany., Doellinger F; Department of Radiology, Charité - Universitätsmedizin Berlin, Berlin, Germany., Zagkla S; Department of Pediatric Respiratory Medicine, Immunology and Critical Care Medicine, Charité - Universitätsmedizin Berlin, Berlin, Germany.; German Center for Child and Adolescent Health (DZKJ), Partner Site Berlin, Berlin, Germany.; German Center for Lung Research (DZL), Associated Partner Site Berlin, Berlin, Germany., Mall MA; Department of Pediatric Respiratory Medicine, Immunology and Critical Care Medicine, Charité - Universitätsmedizin Berlin, Berlin, Germany.; German Center for Child and Adolescent Health (DZKJ), Partner Site Berlin, Berlin, Germany.; German Center for Lung Research (DZL), Associated Partner Site Berlin, Berlin, Germany.; Berlin Institute of Health (BIH) at Charité, Berlin, Germany., Stahl M; Department of Pediatric Respiratory Medicine, Immunology and Critical Care Medicine, Charité - Universitätsmedizin Berlin, Berlin, Germany.; German Center for Child and Adolescent Health (DZKJ), Partner Site Berlin, Berlin, Germany.; German Center for Lung Research (DZL), Associated Partner Site Berlin, Berlin, Germany.; Berlin Institute of Health (BIH) at Charité, Berlin, Germany.
Source: Pediatric pulmonology [Pediatr Pulmonol] 2025 Jun; Vol. 60 (6), pp. e71168.
Publication Type: Journal Article
Journal Info: Publisher: Wiley-Liss Country of Publication: United States NLM ID: 8510590 Publication Model: Print Cited Medium: Internet ISSN: 1099-0496 (Electronic) Linking ISSN: 10990496 NLM ISO Abbreviation: Pediatr Pulmonol Subsets: MEDLINE; In Process
Database: MEDLINE Ultimate
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ISSN:1099-0496
DOI:10.1002/ppul.71168