Hyperphagia in rare melanocortin-4 receptor pathway diseases: therapeutic options and assessing treatment response.

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Bibliographic Details
Title: Hyperphagia in rare melanocortin-4 receptor pathway diseases: therapeutic options and assessing treatment response.
Authors: Argente J; Hospital Infantil Universitario Niño Jesús, Madrid, Spain.; Universidad Autónoma de Madrid, Madrid, Spain.; CIBER Fisiopatología y Nutrición (CIBEROBN), Instituto de Salud Carlos III & IMDEA Food Institute, Madrid, Spain., Clément K; Sorbonne University, Inserm, Nutrition and Obesities; Systemic Approaches, NutriOmique Research Group, Paris, France.; Nutrition Department, Assistance Publique-Hôpitaux de Paris, Pitié-Salpêtrière Hospital, Paris, France., Duis J; RareDiseaseDoc, LLC, Aurora, CO, USA., Farooqi IS; Institute of Metabolic Science and NIHR Cambridge Biomedical Research Centre, University of Cambridge, Cambridge, UK., Kühnen P; Department of Pediatric Endocrinology and Diabetology, Charité-Universitätsmedizin Berlin, Corporate Member of Freie Universität Berlin Und Humboldt-Universität Zu Berlin, Berlin, Germany., Miller JL; Pediatric Endocrinology, Department of Pediatrics, College of Medicine, University of Florida, Gainesville, FL, USA., Roth CL; Seattle Children's Research Institute, Seattle, WA, USA.; Division of Endocrinology, Department of Pediatrics, University of Washington, Seattle, WA, USA., van den Akker E; Erasmus University Medical Center, Rotterdam, The Netherlands. e.l.t.vandenakker@erasmusmc.nl.
Source: Reviews in endocrine & metabolic disorders [Rev Endocr Metab Disord] 2025 Dec; Vol. 26 (6), pp. 917-935. Date of Electronic Publication: 2025 Jun 25.
Publication Type: Journal Article; Systematic Review; Research Support, Non-U.S. Gov't
Journal Info: Publisher: Springer Country of Publication: Germany NLM ID: 100940588 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1573-2606 (Electronic) Linking ISSN: 13899155 NLM ISO Abbreviation: Rev Endocr Metab Disord Subsets: MEDLINE
Database: MEDLINE Ultimate
Description
ISSN:1573-2606
DOI:10.1007/s11154-025-09984-3